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Funding


RCDC

Project Listing by Category


Back to Estimates of Funding for Various Research, Condition, and Disease Categories (RCDC) Click the column headings to sort project listings.
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CategoryFYFunding ICProject NumberSub Project #Project TitlePI NameOrg NameState / CountryAmount
Mucopolysaccharidoses (MPS) 2018 NIAID 5R21AI128087-02 Optimizing Gene Editing in Primary Human B Cells for Therapy and Research MORIARITY, BRANDEN UNIVERSITY OF MINNESOTA MN $191,875
Mucopolysaccharidoses (MPS) 2018 NINDS 5R01NS088766-04 Phenotypic effects of brain-directed enzyme therapy for Sanfilippo B syndrome DICKSON, PATRICIA LA BIOMED RES INST/ HARBOR UCLA MED CTR CA $310,283
Mucopolysaccharidoses (MPS) 2018 NICHD 1R43HD094543-01 Feasibility and validation of an integrated newborn screening algorithm with the targeted Next Generation Sequencing (tNGS) technology as part of a 2nd tier test for Pompe and MPS I BHATTACHARJEE, ARINDAM BAEBIES, INC. NC $215,022
Mucopolysaccharidoses (MPS) 2018 NINDS 5R01NS092671-03 Upregulation of Iduronidase Enzyme in MPSI Disease BROTHERS, SHAUN UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $335,781
Mucopolysaccharidoses (MPS) 2018 NIDDK 2R01DK067859-18 Multiplex Analysis of Inborn Errors of Metabolism GELB, MICHAEL UNIVERSITY OF WASHINGTON WA $603,249
Mucopolysaccharidoses (MPS) 2018 NINDS 5K08NS102398-02 Correction of Mucopolysaccharidosis type 1: Targeting safe harbor loci using genome editing GOMEZ-OSPINA, NATALIA STANFORD UNIVERSITY CA $196,236
Mucopolysaccharidoses (MPS) 2018 NIAMS 1R43AR073543-01 MPS I Skeletal Disease Therapy with Novel Lectin-delivered Replacement Enzyme RADIN, DAVID BIOSTRATEGIES, LC AR $225,000
Mucopolysaccharidoses (MPS) 2018 NINDS 5R01NS102624-02 Optimizing AAV Vectors for Central Nervous System transduction HELDERMON, COY UNIVERSITY OF FLORIDA FL $463,361
Mucopolysaccharidoses (MPS) 2018 NIAMS 5R01AR071975-02 Pathogenesis and Treatment of Bone Disease in the Mucopolysaccharidoses SMITH, LACHLAN UNIVERSITY OF PENNSYLVANIA PA $361,801
Mucopolysaccharidoses (MPS) 2018 NIAMS 5F32AR071298-02 Impaired BMP Signaling and Failed Bone Formation in Mucopolysaccharidosis VII PECK, SUN UNIVERSITY OF PENNSYLVANIA PA $69,586
Mucopolysaccharidoses (MPS) 2018 NICHD 5F30HD081853-04 Novel Dried Blood Spot Mass Spectrometry Functional Assays for Lysosomal Acid Lipase and N-acetylgalactosamine-sulfate Sulfatases for Use in Newborn Screening MASI, SOPHIA UNIVERSITY OF WASHINGTON WA $49,044
Mucopolysaccharidoses (MPS) 2018 NCATS 5U54NS065768-10 5620 Longitudinal Studies of Brain Structure and Function in MPS Disorders WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $45,270
Mucopolysaccharidoses (MPS) 2018 NIDDK 5U54NS065768-10 5620 Longitudinal Studies of Brain Structure and Function in MPS Disorders WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $71,681
Mucopolysaccharidoses (MPS) 2018 NINDS 5U54NS065768-10 5620 Longitudinal Studies of Brain Structure and Function in MPS Disorders WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $51,009
Mucopolysaccharidoses (MPS) 2018 NCATS 5U54NS065768-10 5622 Longitudinal Study of Bone and Endocrine Disease in Children with MPS I, II, and VI: A Multi-Center Study of the Lysosomal Disease Network POLGREEN, LYNDA UNIVERSITY OF MINNESOTA MN $25,878
Mucopolysaccharidoses (MPS) 2018 NIDDK 5U54NS065768-10 5622 Longitudinal Study of Bone and Endocrine Disease in Children with MPS I, II, and VI: A Multi-Center Study of the Lysosomal Disease Network POLGREEN, LYNDA UNIVERSITY OF MINNESOTA MN $40,975
Mucopolysaccharidoses (MPS) 2018 NINDS 5U54NS065768-10 5622 Longitudinal Study of Bone and Endocrine Disease in Children with MPS I, II, and VI: A Multi-Center Study of the Lysosomal Disease Network POLGREEN, LYNDA UNIVERSITY OF MINNESOTA MN $29,158
Mucopolysaccharidoses (MPS) 2018 NCATS 5U54NS065768-10 5624 An Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I CHEN, AGNES UNIVERSITY OF MINNESOTA MN $12,126
Mucopolysaccharidoses (MPS) 2018 NIDDK 5U54NS065768-10 5624 An Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I CHEN, AGNES UNIVERSITY OF MINNESOTA MN $19,201
Mucopolysaccharidoses (MPS) 2018 NINDS 5U54NS065768-10 5624 An Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I CHEN, AGNES UNIVERSITY OF MINNESOTA MN $13,663
Mucopolysaccharidoses (MPS) 2018 NCATS 5U54NS065768-10 5630 Natural History Study for MPS IMC and MPS MID LEVY, PAUL UNIVERSITY OF MINNESOTA MN $2,045
Mucopolysaccharidoses (MPS) 2018 NIDDK 5U54NS065768-10 5630 Natural History Study for MPS IMC and MPS MID LEVY, PAUL UNIVERSITY OF MINNESOTA MN $3,239
Mucopolysaccharidoses (MPS) 2018 NINDS 5U54NS065768-10 5630 Natural History Study for MPS IMC and MPS MID LEVY, PAUL UNIVERSITY OF MINNESOTA MN $2,305
Mucopolysaccharidoses (MPS) 2018 NINDS 5R44NS102086-02 Improving MPS I ERT Efficacy through Lectin-Mediated Delivery RADIN, DAVID BIOSTRATEGIES, LC AR $1,147,007
Mucopolysaccharidoses (MPS) 2018 NINDS 1R21NS104962-01A1 Pharmacologic Induction of IGF2/M6P Receptor-Meidated Transport at the Blood-Brain Barrier for Drug Delivery to the Brain URAYAMA, AKIHIKO UNIVERSITY OF TEXAS HLTH SCI CTR HOUSTON TX $231,000
Mucopolysaccharidoses (MPS) 2018 NINDS 1R43NS108853-01 Intracerebroventricular Iduronidase Delivery to the Brain BROWN, JILLIAN TEGA THERAPEUTICS, INC. CA $225,000
Mucopolysaccharidoses (MPS) 2018 NIGMS 2R44GM115192-02A1 Sleeping Beauty Engineered B Cells for Mucopolysaccharidosis FONTENOT, JASON IMMUSOFT CORPORATION WA $1,028,903
Mucopolysaccharidoses (MPS) 2018 NINDS 2R44NS089061-04 Development and validation of therapy for mucopolysaccharidosis III WOOD, JILL PHOENIX NEST, INC. NY $3,176,406


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