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Funding


RCDC

Project Listing by Category


Back to Estimates of Funding for Various Research, Condition, and Disease Categories (RCDC) Click the column headings to sort project listings.
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CategoryFYFunding ICProject NumberSub Project #Project TitlePI NameOrg NameState / CountryAmount
Gene Therapy 2018 NHLBI 5R42HL099150-04 Lentiviral Vector for the treatment of Fanconi Anemia GOEBEL, WILLIAM RIMEDION, INC. CA $295,259
Gene Therapy 2018 NCI 5R01CA137094-09 Defining Critical p53 Therapeutic Targets and Mechanisms O'SHEA, CLODAGH SALK INSTITUTE FOR BIOLOGICAL STUDIES CA $436,500
Gene Therapy 2018 NIDCD 5R00DC013555-05 Rescue of channelopathy induced anosmias MCINTYRE, JEREMY UNIVERSITY OF FLORIDA FL $248,999
Gene Therapy 2018 NCI 5R01CA175052-05 Enhanced GBM Therapy Using a New Class of HSV Oncolytic Vector GLORIOSO, JOSEPH UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $316,018
Gene Therapy 2018 NCI 5R01CA194064-04 Combination Therapy of OvCA with Oligonucleotides and Photodynamic Therapy MING, XIN WAKE FOREST UNIVERSITY HEALTH SCIENCES NC $283,650
Gene Therapy 2018 NCI 5R01CA200900-03 Systemic RNA Delivery to Tumors SHI, JINJUN BRIGHAM AND WOMEN'S HOSPITAL MA $545,070
Gene Therapy 2018 NIDA 5P30DA033934-05 6609 Mutant Mouse/Viral Vector LICHTMAN, ARON VIRGINIA COMMONWEALTH UNIVERSITY VA $142,737
Gene Therapy 2018 NHLBI 5T32HL007910-19 Basic Sciences Studies on Gene Therapy of Blood Diseases BROXMEYER, HAL INDIANA UNIV-PURDUE UNIV AT INDIANAPOLIS IN $380,561
Gene Therapy 2018 NIAID 5R37AI091476-08 Therapeutic Use of an Enhanced Form of CD4-Ig FARZAN, MICHAEL SCRIPPS FLORIDA FL $943,250
Gene Therapy 2018 NIAID 5R01AI080607-10 Studies in Poxvirus Host Range Genes and Tropism MCFADDEN, GRANT ARIZONA STATE UNIVERSITY-TEMPE CAMPUS AZ $386,250
Gene Therapy 2018 NCI 5P30CA014195-45 7749 PL Mouse HUNTER, TONY SALK INSTITUTE FOR BIOLOGICAL STUDIES CA $43,092
Gene Therapy 2018 NCI 5P30CA014195-45 7759 SR Fun Gen HUNTER, TONY SALK INSTITUTE FOR BIOLOGICAL STUDIES CA $275,643
Gene Therapy 2018 NCI 5P30CA014195-45 7760 SR Gene Therapy HUNTER, TONY SALK INSTITUTE FOR BIOLOGICAL STUDIES CA $144,525
Gene Therapy 2018 NHLBI 5R01HL126850-03 Novel factor VIII variants for improved efficacy in gene therapy for hemophilia A SABATINO, DENISE CHILDREN'S HOSP OF PHILADELPHIA PA $420,000
Gene Therapy 2018 NINDS 5K08NS096219-02 Global AAV gene therapy of Tay-Sachs disease in sheep. EDWARDS, HEATHER AUBURN UNIVERSITY AT AUBURN AL $169,128
Gene Therapy 2018 NCI 5R01CA200844-03 Lipid-dendrimer micellar nanocarriers for siRNA/drug co-delivery in MDR cancer TORCHILIN, VLADIMIR NORTHEASTERN UNIVERSITY MA $349,679
Gene Therapy 2018 NINDS 5P30NS045776-14 7972 Core C Interdepartmental Neuroscience Center BREAKEFIELD, XANDRA MASSACHUSETTS GENERAL HOSPITAL MA $208,005
Gene Therapy 2018 NHLBI 5R01HL125703-04 PET/MRI to study nanotherapy in atherosclerosis MULDER, WILLEM ICAHN SCHOOL OF MEDICINE AT MOUNT SINAI NY $590,721
Gene Therapy 2018 NIDDK 5P30DK041301-29 7944 Core D: Integrated Molecular Technologies KASAHARA, NORIYUKI UNIVERSITY OF CALIFORNIA LOS ANGELES CA $146,969
Gene Therapy 2018 NIAID 5R21AI127381-02 Redirected T Cell Therapy to Cure Invasive Fungal Infections KONTOYIANNIS, DIMITRIOS UNIVERSITY OF TX MD ANDERSON CAN CTR TX $225,008
Gene Therapy 2018 NIAID 5R01AI098446-06 Immunoglobulins Delivered by AVV Vector for the Prevention of SIV Infection DESROSIERS, RONALD UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $731,021
Gene Therapy 2018 NICHD 5R01HD088033-02 Optimizing Therapeutic delivery of MicroRNAs to prevent chronic lung disease in Preterm infants. ROGERS, LYNETTE RESEARCH INST NATIONWIDE CHILDREN'S HOSP OH $319,876
Gene Therapy 2018 NHLBI 5R01HL131143-03 Development of a gene therapy approach to treat acute lung injury using a preclinical, large animal model DEAN, DAVID UNIVERSITY OF ROCHESTER NY $759,156
Gene Therapy 2018 NHLBI 5R01HL130871-03 Development of highly efficient factor VIII mini-gene therapy XIAO, WEIDONG TEMPLE UNIV OF THE COMMONWEALTH PA $482,625
Gene Therapy 2018 NIAID 5R01AI113221-04 Modulating Immunity to Nucleic Acids and Inducing Tolerance by Gene Transfer BROWN, BRIAN ICAHN SCHOOL OF MEDICINE AT MOUNT SINAI NY $421,004
Gene Therapy 2018 NCI 5R01CA174861-05 Novel Theranostics for Pancreatic Cancer DAVYDOVA, JULIA UNIVERSITY OF MINNESOTA MN $319,031
Gene Therapy 2018 NCI 5R01CA196215-03 Systemic Therapy with Infectivity-Selective Oncolytic Adenovirus for PDAC YAMAMOTO, MASATO UNIVERSITY OF MINNESOTA MN $351,132
Gene Therapy 2018 NIAID 5R21AI121993-02 Multifactor mRNA Mediated T Cell Reprogramming for Systemic Lupus Erythematosus KATZ, SAMUEL YALE UNIVERSITY CT $167,500
Gene Therapy 2018 NHLBI 5R01HL131814-02 Novel strategy for Enhancing miRNA as a Therapeutic for Cardiac Regeneration DZAU, VICTOR DUKE UNIVERSITY NC $397,500
Gene Therapy 2018 NIAID 5R01AI128074-02 Restoring Immune Tolerance in a Model of Multiple Sclerosis HOFFMAN, BRAD UNIVERSITY OF FLORIDA FL $381,250
Gene Therapy 2018 NIAID 5R21AI123896-02 Genome Editing to rescue FOXP3 Deficiency in IPEX syndrome BACCHETTA, ROSA STANFORD UNIVERSITY CA $239,135
Gene Therapy 2018 NCI 5R01CA195503-04 Nanoparticle Modified Human Fat Derived Mesenchymal Stem Cells for Brain Cancer (Change of Organization Application) QUINONES-HINOJOSA, ALFREDO MAYO CLINIC JACKSONVILLE FL $363,623
Gene Therapy 2018 NEI 5K08EY026101-03 A nanoparticle platform for targeted delivery of therapeutic agents to retinal pigment epithelial or choroidal endothelial cells YIU, GLENN UNIVERSITY OF CALIFORNIA AT DAVIS CA $206,553
Gene Therapy 2018 NHLBI 5R01HL132840-02 Genetic Repair of Familial Hypercholesterolemia LAGOR, WILLIAM BAYLOR COLLEGE OF MEDICINE TX $581,448
Gene Therapy 2018 NCI 5R01CA211044-02 Off-the-shelf engineered NK cells for the treatment of AML REZVANI, KATY UNIVERSITY OF TX MD ANDERSON CAN CTR TX $366,000
Gene Therapy 2018 NEI 5K08EY023993-05 Molecular Profiling of Rods to Identify New Therapies for Retinal Degenerations WU, DAVID MASSACHUSETTS EYE AND EAR INFIRMARY MA $222,047
Gene Therapy 2018 NIMH 5R01MH106460-03 Selective HDAC inhibition and therapeutic target genes: Identification of novel treatments for Bipolar Disorder MCCLUNG, COLLEEN UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $381,144
Gene Therapy 2018 NEI 5R01EY013433-11 A Ribozyme Rescue Strategy for Autosomal Dominant Retinitis Pigmentosa SULLIVAN, JOHN STATE UNIVERSITY OF NEW YORK AT BUFFALO NY $378,000
Gene Therapy 2018 NEI 5R01EY024958-04 CONVERTING BIPOLAR CELLS INTO RED-SHIFTED OPTOGENETIC SENSORS FOR RETINAL THERAPY CORBO, JOSEPH WASHINGTON UNIVERSITY MO $419,657
Gene Therapy 2018 NIDA 5P01DA008227-26 7218 ANIMAL MODEL CORE NESTLER, ERIC ICAHN SCHOOL OF MEDICINE AT MOUNT SINAI NY $322,865
Gene Therapy 2018 NCI 5P30CA008748-52 7556 Gene Transfer RIVIERI, ISABELLE SLOAN-KETTERING INST CAN RESEARCH NY $369,891
Gene Therapy 2018 NIAID 5R21AI128087-02 Optimizing Gene Editing in Primary Human B Cells for Therapy and Research MORIARITY, BRANDEN UNIVERSITY OF MINNESOTA MN $191,875
Gene Therapy 2018 NIGMS 5R01GM119186-02 Mechanism of high-efficiency transduction of hepatocytes by optimized AAV vectors LING, CHEN UNIVERSITY OF FLORIDA FL $293,563
Gene Therapy 2018 NINDS 5F32NS095515-03 Treatment of Peripheral Nervous System Dysfunction in Giant Axonal Neuropathy BAILEY, RACHEL UNIV OF NORTH CAROLINA CHAPEL HILL NC $61,174
Gene Therapy 2018 NIAID 7R03AI131072-02 Genetic Engineering of the rotavirus genome through a fully recombinant reverse gene PATTON, JOHN INDIANA UNIVERSITY BLOOMINGTON IN $78,750
Gene Therapy 2018 NIGMS 5R01GM108073-04 Pre-clinical studies of novel mitochondrial gene therapies PALLADINO, MICHAEL UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $286,768
Gene Therapy 2018 NIDA 5DP1DA039560-04 Reversing HIV T cell dysfunction by aptamer targeting of therapeutic siRNAs GILBOA, ELI UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $767,500
Gene Therapy 2018 NIDCD 5R01DC014496-03 Gene Therapy for Treating Human Genetic Deafness Tested in Animal Models LIN, XI EMORY UNIVERSITY GA $481,848
Gene Therapy 2018 NCI 5F31CA213668-02 CD40L-Modified Chimeric Antigen Receptor (CAR) T Cells KUHN, NICHOLAS SLOAN-KETTERING INST CAN RESEARCH NY $44,524
Gene Therapy 2018 NIDDK 5R01DK102861-04 Translational study of miR-146a gene therapy for diabetic peripheral neuropathy LIU, XIANSHUANG HENRY FORD HEALTH SYSTEM MI $334,125
Gene Therapy 2018 NIA 5R37AG008796-27 Slow Outward Currents and Learning In Aging Hippocampus DISTERHOFT, JOHN NORTHWESTERN UNIVERSITY AT CHICAGO IL $569,055
Gene Therapy 2018 NHLBI 5R01HL134839-02 In Vivo RNA-Mediated Gene Editing of Hemophilia A WEISSMAN, DREW UNIVERSITY OF PENNSYLVANIA PA $730,924
Gene Therapy 2018 NHLBI 5R01HL136135-02 Novel Gene Editing Approaches for Hemoglobinopathies KIEM, HANS-PETER FRED HUTCHINSON CANCER RESEARCH CENTER WA $921,786
Gene Therapy 2018 NCI 5R01CA196796-03 DNA-specific pattern recognition receptor activation following DNA electroporation HELLER, LOREE OLD DOMINION UNIVERSITY VA $316,169
Gene Therapy 2018 NIDDK 5R01DK090058-08 Lentiviral-transduced hematopoictic stem cell transplantation for cystinosis CHERQUI, STEPHANIE UNIVERSITY OF CALIFORNIA, SAN DIEGO CA $348,750
Gene Therapy 2018 NIAID 5R01AI029329-28 Enhancing the Intracellular Functioning of anti-HV RNAS ROSSI, JOHN BECKMAN RESEARCH INSTITUTE/CITY OF HOPE CA $654,174
Gene Therapy 2018 NCI 5R01CA193140-03 Targeting the Ig-light chains with CAR-T cells in lymphoid tumors DOTTI, GIANPIETRO UNIV OF NORTH CAROLINA CHAPEL HILL NC $511,190
Gene Therapy 2018 NIBIB 5R01EB022148-03 Cancer-specific nanoparticle-mediated gene therapy to treat hepatocellular carcinoma GREEN, JORDAN JOHNS HOPKINS UNIVERSITY MD $364,500
Gene Therapy 2018 NICHD 5R01HD083680-04 Mechanisms of cognitive deficits in dystroglycanopathies HU, HUAIYU UPSTATE MEDICAL UNIVERSITY NY $563,377
Gene Therapy 2018 NHLBI 2T32HL092332-16 Training In Cell and Gene Therapy HESLOP, HELEN BAYLOR COLLEGE OF MEDICINE TX $353,720
Gene Therapy 2018 NHLBI 2P01HL066299-16A1 8840 Gene Delivery Core ALEXEYEV, MIKHAIL UNIVERSITY OF SOUTH ALABAMA AL $288,627
Gene Therapy 2018 NIAAA 5K01AA024174-03 Connective tissue growth factor: an intriguing therapeutic target in alcoholic liver disease PI, LIYA UNIVERSITY OF FLORIDA FL $145,057
Gene Therapy 2018 NIDCR 5R01DE025681-03 Nanolipidoids-Conjugated MicroRNA Enhance Oral and Cranial Bone Regeneration CHEN, JAKE TUFTS UNIVERSITY BOSTON MA $330,000
Gene Therapy 2018 NIAID 5R43AI125043-02 Screening for rAAV transduction enhancers BOWLIN, TERRY MICROBIOTIX, INC MA $290,608
Gene Therapy 2018 NCI 1P50CA210964-01A1 5547 Project 4: Immunovirotherapy VILE, RICHARD MAYO CLINIC ROCHESTER MN $321,665
Gene Therapy 2018 NCI 2P50CA107399-11A1 5660 GMP Manufacturing KWAK, LARRY BECKMAN RESEARCH INSTITUTE/CITY OF HOPE CA $313,709
Gene Therapy 2018 NCI 2P50CA107399-11A1 5661 CMV/CD19 bi-Specific CAR T cells combined with CMV vaccine as post-transplantation immunotherapy for non-Hodgkin lymphoma FORMAN, STEPHEN BECKMAN RESEARCH INSTITUTE/CITY OF HOPE CA $281,345
Gene Therapy 2018 NHLBI 5R01HL021796-31 Mechanisms of Prosthetic Arterial Bypass Graft Failure LOGERFO, FRANK BETH ISRAEL DEACONESS MEDICAL CENTER MA $749,995
Gene Therapy 2018 NHLBI 5R01HL134321-03 Intraosseous delivery of lentiviral vectors for hemophilia A gene therapy MIAO, CAROL SEATTLE CHILDREN'S HOSPITAL WA $627,844
Gene Therapy 2018 NIBIB 5F32EB023101-02 Sequence- and Stereocontrolled Triazolium-containing Precise Polymers for siRNA Complexation and Delivery GOLDER, MATTHEW MASSACHUSETTS INSTITUTE OF TECHNOLOGY MA $59,038
Gene Therapy 2018 NEI 1R01EY028553-01 Using functional homology of RP1 isoforms to guide alternative therapeutic strategies FARKAS, MICHAEL STATE UNIVERSITY OF NEW YORK AT BUFFALO NY $322,299
Gene Therapy 2018 NHLBI 5R01HL136721-02 Genome edited iPS cell-derived macrophages as a novel lung cell therapy SUZUKI, TAKUJI CINCINNATI CHILDRENS HOSP MED CTR OH $390,000
Gene Therapy 2018 NHLBI 1R01HL140295-01 Clinical trial of AAV8-mediated FVIII gene transfer for hemophilia A DAVIDOFF, ANDREW ST. JUDE CHILDREN'S RESEARCH HOSPITAL TN $561,582
Gene Therapy 2018 NIAID 1R01AI135953-01 Targeting a Novel Hematopoietic Stem Cell Population in Non-Human Primates for Effective and Sustained Gene Therapy KIEM, HANS-PETER FRED HUTCHINSON CANCER RESEARCH CENTER WA $909,598
Gene Therapy 2018 NIAID 5F32AI126943-02 Allograft rejection and salvage therapy with chimeric antigen receptor T-regulatory cells in murine hindlimb transplant CONKLING, NICOLE UNIVERSITY OF CALIFORNIA, SAN FRANCISCO CA $66,790
Gene Therapy 2018 NIBIB 5R21EB023369-02 Immunomodulation through Nanocapsule-Mediated Cytosolic Delivery of siRNA ROTELLO, VINCENT UNIVERSITY OF MASSACHUSETTS AMHERST MA $229,903
Gene Therapy 2018 NINDS 5R01NS088667-04 Disseminated gene delivery to the CNS by human iPSC-derived neural stem cells WOLFE, JOHN CHILDREN'S HOSP OF PHILADELPHIA PA $367,500
Gene Therapy 2018 NHLBI 5R01HL130040-03 In Vivo Hematopoietic Stem Cell Gene Therapy of Beta-Thalassemia LIEBER, ANDRE UNIVERSITY OF WASHINGTON WA $386,250
Gene Therapy 2018 NIBIB 5R01EB018956-04 Thermal Assisted Gene Electro Transfer to the Skin HELLER, RICHARD OLD DOMINION UNIVERSITY VA $344,250
Gene Therapy 2018 NIAID 5R01AI116698-04 Selection of New rAAV Vectors Using Replicating Viral Capsids Libraries KAY, MARK STANFORD UNIVERSITY CA $593,119
Gene Therapy 2018 NCI 5R21CA212731-02 Nanoneedle microrobots for single cancer cell manipulation and genome editing DAVIS, RONALD STANFORD UNIVERSITY CA $314,000
Gene Therapy 2018 NCI 1R01CA223788-01 Nanotherapeutics for Synergistic Targeting of Myc in Prostate Cancer LI, SONG UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $354,559
Gene Therapy 2018 NIBIB 1R21EB025490-01 Harnessing the gap junction network for direct intracellular delivery of siRNA and chemotherapeutics STACHOWIAK, JEANNE UNIVERSITY OF TEXAS, AUSTIN TX $227,878
Gene Therapy 2018 NIDCD 5R21DC016157-02 Cochlear angiogenesis SHI, XIAO-RUI OREGON HEALTH & SCIENCE UNIVERSITY OR $192,500
Gene Therapy 2018 NIDDK 5R01DK112836-02 Endogenous alpha-to-beta cell transdifferentiation in diabetes GITTES, GEORGE UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $373,601
Gene Therapy 2018 NIBIB 5R01EB020147-04 MRI-Guided miRNA Nanoparticle Delivery to Glioblastoma With Focused Ultrasound PRICE, RICHARD UNIVERSITY OF VIRGINIA VA $612,150
Gene Therapy 2018 OD 5R01OD023700-02 Development of epidermal progenitor cell-based therapy for regenerative medicine WU, XIAOYANG UNIVERSITY OF CHICAGO IL $405,000
Gene Therapy 2018 NIMH 5R01MH102144-05 Validation of the Rev-dependent vector for targeting SIV macrophage reservoirs WU, YUNTAO GEORGE MASON UNIVERSITY VA $652,436
Gene Therapy 2018 NIDDK 2P30DK017047-42 7678 Vector and Transgenic Mouse Core BORNFELDT, KARIN UNIVERSITY OF WASHINGTON WA $235,629
Gene Therapy 2018 NIAMS 5R01AR040864-29 Dystrophin Replacement CHAMBERLAIN, JEFFREY UNIVERSITY OF WASHINGTON WA $576,032
Gene Therapy 2018 NCI 5R01CA187923-04 Novel Strategies to Potentiate a Ras-targeted Oncolytic Herpes Simplex Virus ZHANG, XIAOLIU UNIVERSITY OF HOUSTON TX $344,023
Gene Therapy 2018 NIAID 5R01AI117408-03 Enhance AAV Liver Transduction with Capsid Immune Evasion LI, CHENGWEN UNIV OF NORTH CAROLINA CHAPEL HILL NC $380,000
Gene Therapy 2018 NIGMS 5R01GM088351-08 The mechanism of Cas9/CRISPR-initiated genome modification in human somatic cells HENDRICKSON, ERIC UNIVERSITY OF MINNESOTA MN $283,657
Gene Therapy 2018 NHLBI 5R33HL120760-05 Lipidomic Screening For Functional Surfactant Gene Mutations COLE, FRANCIS WASHINGTON UNIVERSITY MO $459,059
Gene Therapy 2018 NIGMS 5R01GM115911-03 Engineered Cas9 Nucleases with Single-Genomic-Site Precision for CYBB Correction WOLFE, SCOT UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $398,059
Gene Therapy 2018 NCI 1R03CA223886-01 Safety and anti-tumor activity of B7-H3 CAR T cells in TNBC FERRONE, SOLDANO MASSACHUSETTS GENERAL HOSPITAL MA $96,719
Gene Therapy 2018 NCI 5R01CA207407-02 Generating rapid antitumor immunity with lymphocyte-reprogramming nanocarriers STEPHAN, MATTHIAS FRED HUTCHINSON CANCER RESEARCH CENTER WA $371,925
Gene Therapy 2018 NCI 5R01CA208783-02 Systemic RNA interference to reactivate p53 tumor suppression STEGH, ALEXANDER NORTHWESTERN UNIVERSITY AT CHICAGO IL $361,766
Gene Therapy 2018 NIDCD 2R01DC000188-37 Single-Neuron Marking in the Study of Abnormal Cochleas LIBERMAN, M. MASSACHUSETTS EYE AND EAR INFIRMARY MA $649,635
Gene Therapy 2018 NIDA 5R01DA034749-05 Neuropathic mechanisms and gene therapy on opioid dependence HAO, SHUANGLIN UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $345,452
Gene Therapy 2018 NCI 5R01CA200507-02 Optimizing Delivery of Oncolytic Measles Virus Strains with Cell Carriers GALANIS, EVANTHIA MAYO CLINIC ROCHESTER MN $592,664
Gene Therapy 2018 NINDS 2R01NS032677-25A1 Genetically Engineered Viruses for Brain Tumor Therapy MARTUZA, ROBERT MASSACHUSETTS GENERAL HOSPITAL MA $548,365
Gene Therapy 2018 NINDS 5R03NS101682-02 Investigation of Neuroanatomical Alterations in Arginase Deficiency After Neonatal Gene Therapy LIPSHUTZ, GERALD UNIVERSITY OF CALIFORNIA LOS ANGELES CA $77,000
Gene Therapy 2018 NHLBI 5R01HL127413-04 Biodegradable Mucus Penetrating DNA Nanoparticle for Gene Therapy of CF HANES, JUSTIN JOHNS HOPKINS UNIVERSITY MD $396,283
Gene Therapy 2018 NCI 1R01CA217059-01A1 Imaging-guided fine tuning of CAR T cell affinity to limit T cell cytotoxicity to tumor antigen JIN, MOONSOO WEILL MEDICAL COLL OF CORNELL UNIV NY $525,684
Gene Therapy 2018 NIAID 1R01AI130123-01A1 Host determinants of adeno-associated virus entry and trafficking CARETTE, JAN STANFORD UNIVERSITY CA $392,500
Gene Therapy 2018 NINDS 5R01NS100979-02 Cell and Gene Replacement Strategies for Arginase Deficiency LIPSHUTZ, GERALD UNIVERSITY OF CALIFORNIA LOS ANGELES CA $329,579
Gene Therapy 2018 NIBIB 1R01EB023878-01A1 Controlled Delivery of Plasmid DNA via Low-Temperature Ion Deposition HELLER, RICHARD OLD DOMINION UNIVERSITY VA $424,746
Gene Therapy 2018 NHLBI 2R01HL089221-10 Determinants of AAV Tropism ASOKAN, ARAVIND DUKE UNIVERSITY NC $622,381
Gene Therapy 2018 NEI 1R01EY027763-01A1 Molecular mechanisms of translational control in mice with inherited retinal degeneration GORBATYUK, MARINA UNIVERSITY OF ALABAMA AT BIRMINGHAM AL $371,250
Gene Therapy 2018 NEI 1R01EY027767-01A1 Vascular Gene Delivery and Early Disease Biomarkers in Diabetic Retinopathy LIPINSKI, DANIEL MEDICAL COLLEGE OF WISCONSIN WI $372,844
Gene Therapy 2018 NHLBI 1R01HL135287-01A1 In vivo gene editing of hematopoietic stem and progenitor cells WAGERS, AMY JOSLIN DIABETES CENTER MA $432,401
Gene Therapy 2018 NIAID 5R01AI065429-14 Innate immunity to adenovirus SHAYAKHMETOV, DMITRY EMORY UNIVERSITY GA $390,000
Gene Therapy 2018 NCI 5R01CA175318-04 A Nanotechnology Platform for Suicide Gene Therapy of Recurring Ovarian Cancer HATEFI, ARASH RUTGERS, THE STATE UNIV OF N.J. NJ $354,563
Gene Therapy 2018 NCI 5R21CA210202-02 Targeting melanoma hypoxia with lactic acid bacterium L. lactis GOMEZ-GUTIERREZ, JORGE UNIVERSITY OF LOUISVILLE KY $167,475
Gene Therapy 2018 NINDS 5F32NS093898-03 Lentiviral-mediated Hematopoietic Stem Cell Gene Therapy for Canine Globoid Cell Leukodystrophy BRADBURY, ALLISON UNIVERSITY OF PENNSYLVANIA PA $35,334
Gene Therapy 2018 NIAMS 5R21AR071633-02 Chimeric antigen receptor (CAR) therapy for autoimmune arthritis ROSLONIEC, EDWARD UNIVERSITY OF TENNESSEE HEALTH SCI CTR TN $166,320
Gene Therapy 2018 NINDS 5R01NS086352-05 PGC-1alpha and Pitx3 as individual and combined targets for neuroprotection SIMON, DAVID BETH ISRAEL DEACONESS MEDICAL CENTER MA $379,991
Gene Therapy 2018 NCI 5R01CA150153-09 Enhancing viral oncolysis with vasculostatin gene delivery KAUR, BALVEEN UNIVERSITY OF TEXAS HLTH SCI CTR HOUSTON TX $382,987
Gene Therapy 2018 NEI 5R01EY008123-30 Photoreceptor Ciliopathies: UNC119 Paralogs and NPHP10/NPHP5 BAEHR, WOLFGANG UNIVERSITY OF UTAH UT $372,500
Gene Therapy 2018 NEI 5R01EY026682-03 Mechanistic Studies on Regenerative Medicine Approaches to Childhood Blindness BASSUK, ALEXANDER UNIVERSITY OF IOWA IA $389,825
Gene Therapy 2018 NIBIB 1K99EB023979-01A1 Non-viral delivery of CRISPR/Cas9 for targeted gene replacement NELSON, CHRISTOPHER DUKE UNIVERSITY NC $86,114
Gene Therapy 2018 NCI 1R01CA224304-01 Self-assembled multifunctional aptamer-complex biomaterial for precision medicine ZU, YOULI METHODIST HOSPITAL RESEARCH INSTITUTE TX $369,431
Gene Therapy 2018 NCI 5R01CA056821-24 Immunization Against Melanoma Differentiation Antigens WOLCHOK, JEDD SLOAN-KETTERING INST CAN RESEARCH NY $299,950
Gene Therapy 2018 NCI 5R01CA203852-03 Reconstruction of an oncolytic HSV vector for systemic delivery ZHANG, XIAOLIU UNIVERSITY OF HOUSTON TX $346,450
Gene Therapy 2018 NCI 5R01CA217179-02 A Phase 1 Study of M032, a Genetically Engineered HSV-1 Expressing IL-12, in Patients with Recurrent/Progressive Glioblastoma Multiforme, Anaplastic Astrocytoma, or Gliosarcoma. MARKERT, JAMES UNIVERSITY OF ALABAMA AT BIRMINGHAM AL $559,312
Gene Therapy 2018 NIDDK 5F31DK108624-03 Hemophilia B Gene Therapy via CRISPR/Cas9-Targeted Integration of the Factor IX Gene using Adenovirus Vector Delivery STEPHENS, CALVIN WASHINGTON UNIVERSITY MO $31,131
Gene Therapy 2018 NINDS 5R01NS095817-03 Systemic gene therapy for glioblastoma ZHOU, JIANGBING YALE UNIVERSITY CT $364,219
Gene Therapy 2018 NINDS 5F31NS098540-02 A Personalized Gene Therapy Approach for Charcot-Marie-Tooth Disease MORELLI, KATHRYN JACKSON LABORATORY ME $34,730
Gene Therapy 2018 NCI 5R21CA204036-02 In vivo anti-PD1 gene therapy LIEBER, ANDRE UNIVERSITY OF WASHINGTON WA $168,970
Gene Therapy 2018 NIAID 2R01AI051390-17 Immunology of factor IX Gene Transfer to Liver HERZOG, ROLAND UNIVERSITY OF FLORIDA FL $159,160
Gene Therapy 2018 NINDS 1R35NS105068-01 Preclinical development of breakthrough immunotherapy for brain tumors OKADA, HIDEHO UNIVERSITY OF CALIFORNIA, SAN FRANCISCO CA $601,887
Gene Therapy 2018 NIAID 5U01AI131296-02 Therapeutic vaccination and PD-1 blockade in treated HIV disease DEEKS, STEVEN UNIVERSITY OF CALIFORNIA, SAN FRANCISCO CA $1,370,393
Gene Therapy 2018 NCI 5R01CA183040-05 Ovarian cancer gene therapy using HPV pseudovirion WU, TZYY-CHOOU JOHNS HOPKINS UNIVERSITY MD $336,150
Gene Therapy 2018 NCI 5R01CA190144-04 Liver Cancer Risk with rAAV Gene Therapy GROMPE, MARKUS OREGON HEALTH & SCIENCE UNIVERSITY OR $586,035
Gene Therapy 2018 NCI 5R01CA196947-03 Disrupting tumor/bone malignant interactions with multifunctional cytokine sonodelivery FIGUEIREDO, MARXA PURDUE UNIVERSITY IN $349,968
Gene Therapy 2018 NCI 1F32CA224438-01 Creating a targeted micropharmacy for improved cellular cancer therapies GARDNER, THOMAS SLOAN-KETTERING INST CAN RESEARCH NY $58,654
Gene Therapy 2018 NIAMS 5R01AR067491-04 Inhibition of NF-kB with siRNA/Peptide Nanoparticles for Arthritis Treatment PHAM, CHRISTINE WASHINGTON UNIVERSITY MO $362,701
Gene Therapy 2018 NCI 5R01CA204720-03 In vivo imaging of the stem cell loaded oncolytic viruses for cancer therapy SHAH, KHALID BRIGHAM AND WOMEN'S HOSPITAL MA $386,339
Gene Therapy 2018 NCI 5R01CA204968-03 Targeted Delivery of Brain Penetrating DNA Nanoparticles to Brain Tumors HANES, JUSTIN JOHNS HOPKINS UNIVERSITY MD $506,098
Gene Therapy 2018 NHLBI 5R01HL136652-02 Biodegradable nanoparticles, a genome editing platform to treat hemophilia DONG, YIZHOU OHIO STATE UNIVERSITY OH $392,468
Gene Therapy 2018 NEI 1R24EY027285-01A1 Translational Gene Therapy for CNGB1 Retinitis Pigmentosa PETERSEN-JONES, SIMON MICHIGAN STATE UNIVERSITY MI $1,253,534
Gene Therapy 2018 NCI 5P30CA086862-18 7658 Cluster A: 2 Viral Vector Core SINN, PATRICK UNIVERSITY OF IOWA IA $67,762
Gene Therapy 2018 NCI 5R01CA186730-04 Efficient Delivery of Plasmid DNA to Achieve Appropriate Transgene Expression HELLER, RICHARD OLD DOMINION UNIVERSITY VA $359,454
Gene Therapy 2018 NIDDK 5P30DK054759-19 7715 Administrative Core ENGELHARDT, JOHN UNIVERSITY OF IOWA IA $112,063
Gene Therapy 2018 NIDDK 5P30DK054759-19 7716 Vector Core MCCRAY, PAUL UNIVERSITY OF IOWA IA $167,707
Gene Therapy 2018 NIDDK 5P30DK054759-19 7717 Animal Models Core ENGELHARDT, JOHN UNIVERSITY OF IOWA IA $266,047
Gene Therapy 2018 NIDDK 5P30DK054759-19 7718 Comparative Pathology Core GIBSON-CORLEY, KATHERINE UNIVERSITY OF IOWA IA $122,407
Gene Therapy 2018 NIDDK 5P30DK054759-19 7719 Cells and Tissue Core ZABNER, JOSEPH UNIVERSITY OF IOWA IA $167,707
Gene Therapy 2018 NIDDK 5P30DK054759-19 7720 Clinical Core STARNER, TIMOTHY UNIVERSITY OF IOWA IA $92,207
Gene Therapy 2018 NIDDK 5P30DK054759-19 7721 Pilot and Feasibility ENGELHARDT, JOHN UNIVERSITY OF IOWA IA $215,612
Gene Therapy 2018 NEI 5R01EY025287-03 Plasticity of the human visual system studied in response to retinal gene therapy ASHTARI, MANZAR UNIVERSITY OF PENNSYLVANIA PA $522,525
Gene Therapy 2018 NEI 5R01EY027414-02 Intravenous MitoTargeted AAV9 Gene Therapy for Treatment of Visual Loss and Encephalopathy in Leigh Syndrome and NARP GUY, JOHN UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $383,750
Gene Therapy 2018 NIBIB 1R21EB024308-01A1 Bioengineering of vein grafts to resist intimal hyperplasia FERRAN, CHRISTIANE BETH ISRAEL DEACONESS MEDICAL CENTER MA $262,500
Gene Therapy 2018 NEI 5U10EY023558-05 Leber's Hereditary Optic Neuropathy: Gene Therapy Clinical Trial GUY, JOHN UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $1
Gene Therapy 2018 NEI 5R01EY026564-03 Targeting Retinitis Pigmentosa Using Nanoparticle-Mediated Delivery of Genomic DNA HAN, ZONGCHAO UNIV OF NORTH CAROLINA CHAPEL HILL NC $374,152
Gene Therapy 2018 NINDS 5R01NS088399-05 AAV capsid functions, immune evasion and neuronal targeting in mice and NHP NAKAI, HIROYUKI OREGON HEALTH & SCIENCE UNIVERSITY OR $336,875
Gene Therapy 2018 NINDS 5R01NS093941-03 Whole-body therapy for GM2 gangliosidoses MARTIN, DOUGLAS AUBURN UNIVERSITY AT AUBURN AL $589,446
Gene Therapy 2018 NIAMS 5R01AR069085-03 CRISPR/Cas9-Based Gene Editing for the Correction of Duchenne Muscular Dystrophy GERSBACH, CHARLES DUKE UNIVERSITY NC $339,430
Gene Therapy 2018 NIAMS 5R01AR057076-07 Regional Gene Therapy to Enhance Bone Repair LIEBERMAN, JAY UNIVERSITY OF SOUTHERN CALIFORNIA CA $425,868
Gene Therapy 2018 NHLBI 5U19HL129902-04 5441 Admin Core CANNON, PAULA UNIVERSITY OF SOUTHERN CALIFORNIA CA $169,147
Gene Therapy 2018 NHLBI 5U19HL129902-04 5442 NHP Model and Transplantation Core HU, SHIU-LOK UNIVERSITY OF WASHINGTON WA $485,926
Gene Therapy 2018 NHLBI 5U19HL129902-04 5443 Integrated Functional Genomics SEKALY, RAFICK- CASE WESTERN RESERVE UNIVERSITY OH $236,571
Gene Therapy 2018 NHLBI 5U19HL129902-04 5444 Defining HIV sanctuary sites during autologous and allogeneic transplantation KEAN, LESLIE SEATTLE CHILDREN'S HOSPITAL WA $894,352
Gene Therapy 2018 NHLBI 5U19HL129902-04 5445 Precision gene editing for HIV gene therapy CANNON, PAULA UNIVERSITY OF SOUTHERN CALIFORNIA CA $68,728
Gene Therapy 2018 NHLBI 5U19HL129902-04 5446 Overcoming barriers to efficient genome editing in HSPCs GREGORY, PHILIP SANGAMO BIOSCIENCES, INC. CA $144,349
Gene Therapy 2018 NHLBI 5U19HL129902-04 5447 Stem cell expansion and gene editing in a nonhuman primate model of HIV/AIDS KIEM, HANS-PETER FRED HUTCHINSON CANCER RESEARCH CENTER WA $530,022
Gene Therapy 2018 NEI 5U10EY024247-05 Biostatistics Center for Leber's Hereditary Optic Neuropathy: Gene Therapy Trial FEUER, WILLIAM UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $116,387
Gene Therapy 2018 NHLBI 5R01HL122332-04 Therapeutic potential for AAV/micro-dystrophin transfer to cardiopulmonary tissue CHAMBERLAIN, JEFFREY UNIVERSITY OF WASHINGTON WA $503,928
Gene Therapy 2018 NHLBI 1R42HL140670-01 Oxidation-resistant Anti-protease Therapy CRYSTAL, RONALD LEXEO THERAPEUTICS, LLC NY $224,967
Gene Therapy 2018 NIAID 1R41AI136225-01 Numeric Expansion of CD-19 Specific T cells in Magnetic 3D Culture TSENG, HUBERT NANO3D BIOSCIENCES, INC. TX $175,849
Gene Therapy 2018 NCI 1R41CA224652-01 Innovative TME-specific Pro-CAR T-cells for Immunotherapy of Solid Tumors LI, JINGJING PANACISE BIO, INC. NC $224,991
Gene Therapy 2018 NIAID 1R43AI136163-01 Cpf1-mediated inactivation of an AAV transgene ALPERT, MICHAEL EMMUNE, INC FL $300,000
Gene Therapy 2018 NIAID 1R43AI140784-01 Design and Optimization of Clinical Gene Gun for Delivery of Nucleic Acid Vaccines MUNSON, PAUL ORLANCE, INC. WA $300,000
Gene Therapy 2018 NIAMS 5R01AR044533-23 Assembly of the Dystrophin-Glycoprotein Complex CHAMBERLAIN, JEFFREY UNIVERSITY OF WASHINGTON WA $523,923
Gene Therapy 2018 NCI 5R44CA188154-03 Next generation CRISPR/Cas9-RNAi mouse models for accelerated drug discovery research PREMSRIRUT, PREM MIRIMUS, INC. NY $751,587
Gene Therapy 2018 NIAMS 5R01AR067247-03 Collagen turnover-stimulated gene delivery to enhance chronic wound repair SULLIVAN, MILLICENT UNIVERSITY OF DELAWARE DE $343,622
Gene Therapy 2018 NIAID 5U19AI117941-04 5326 Administrative Core CHEN, IRVIN UNIVERSITY OF CALIFORNIA LOS ANGELES CA $140,047
Gene Therapy 2018 NIAID 5U19AI117941-04 5327 Viral Immunology Core YANG, OTTO UNIVERSITY OF CALIFORNIA LOS ANGELES CA $144,203
Gene Therapy 2018 NIAID 5U19AI117941-04 5328 Improve the engraftment of combinatorial anti-HIV-1 gene modified HSPC AN, DONG SUNG UNIVERSITY OF CALIFORNIA LOS ANGELES CA $291,449
Gene Therapy 2018 NIAID 5U19AI117941-04 5329 Tracking the clonal behavior of repopulating cells CHEN, IRVIN UNIVERSITY OF CALIFORNIA LOS ANGELES CA $289,472
Gene Therapy 2018 NIAID 5U19AI117941-04 5330 Characterization of CAR-directed T-cells to suppress HIV-1 in vivo KITCHEN, SCOTT UNIVERSITY OF CALIFORNIA LOS ANGELES CA $434,455
Gene Therapy 2018 NIAID 5U19AI117941-04 5331 Pre-clinical development of gene modified stem cells and CAR T-cells for HIV-1 SYMONDS, GEOFFREY CALIMMUNE, INC. AZ $656,836
Gene Therapy 2018 NHLBI 5R01HL128139-04 Development of clinically feasible Ultrasound-mediated gene therapy for hemophilia MIAO, CAROL SEATTLE CHILDREN'S HOSPITAL WA $463,181
Gene Therapy 2018 NIAID 1R21AI136100-01 Genetically Modified Gamma Delta T Cells to Target SIV Reservoirs ROUT, NAMITA TULANE UNIVERSITY OF LOUISIANA LA $230,928
Gene Therapy 2018 NICHD 1R21HD091461-01A1 T cell-mediated Gene Replacement Therapy BROWN, BRIAN ICAHN SCHOOL OF MEDICINE AT MOUNT SINAI NY $251,737
Gene Therapy 2018 NIAAA 5R01AA024757-03 GDNF gene therapy to block relapse of heavy alcohol use in monkeys FORD, MATTHEW OREGON HEALTH & SCIENCE UNIVERSITY OR $433,009
Gene Therapy 2018 NIDDK 5R01DK102767-04 Low Electric Field-Based Gene Delivery of IL-30 Gene Therapy for Liver Injury LI, SHULIN UNIVERSITY OF TX MD ANDERSON CAN CTR TX $360,000
Gene Therapy 2018 NINDS 5R01NS097726-03 Developing a drug-inducible gene therapy for temporal lobe epilepsy PEREZ-REYES, EDWARD UNIVERSITY OF VIRGINIA VA $345,625
Gene Therapy 2018 NCI 1U01CA224766-01 Protective Role of Nonclassical Monocytes in Immunotherapies for Solid Cancers HEDRICK, CATHERINE LA JOLLA INST FOR ALLERGY & IMMUNOLGY CA $418,320
Gene Therapy 2018 NHLBI 5R01HL134510-03 Therapeutic potential of CRISPR/Cas9 genome engineering in humanized mouse models BISSIG, KARL-DIMITER BAYLOR COLLEGE OF MEDICINE TX $599,025
Gene Therapy 2018 NHLBI 5R01HL136375-02 New Chromatin Insulators and Enhancers for Gene Therapy of the Hemoglobinopathies STAMATOYANNOPOULOS, THALIA UNIVERSITY OF WASHINGTON WA $579,627
Gene Therapy 2018 NINDS 5R01NS064404-09 Ultrasound-aided gene transfer to direct cortical neurogenesis after brain injury PUN, SUZIE UNIVERSITY OF WASHINGTON WA $438,657
Gene Therapy 2018 NHLBI 5R01HL102035-09 Platelet-derived FVIII Gene Therapy of Hemophilia A SHI, QIZHEN MEDICAL COLLEGE OF WISCONSIN WI $366,156
Gene Therapy 2018 NINDS 5F32NS095508-03 Enhancing siRNA delivery and efficacy in the brain through conjugation of bioactive, polyunsaturated fatty acids OSBORN, MAIRE UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $62,034
Gene Therapy 2018 NIA 5R03AG055899-02 Restore energy capacity in the aging heart YANG, QINGLIN UNIVERSITY OF ALABAMA AT BIRMINGHAM AL $74,250
Gene Therapy 2018 NEI 5R01EY017294-11 Gene Therapy in the Cornea MOHAN, RAJIV UNIVERSITY OF MISSOURI-COLUMBIA MO $380,735
Gene Therapy 2018 NHLBI 5P01HL032262-36 7749 Project 1 BCL11A Protein in Hemoglobin Regulation, Stuart H. Orkin ORKIN, STUART BOSTON CHILDREN'S HOSPITAL MA $430,810
Gene Therapy 2018 NHLBI 5R01HL123326-03 Direct in vivo bone marrow transfer of lentiviral vector to correct hemophilia A MIAO, CAROL SEATTLE CHILDREN'S HOSPITAL WA $482,250
Gene Therapy 2018 NHLBI 5P01HL091799-10 7161 Gene Vector Core RABIONOWITZ, JOSEPH TEMPLE UNIV OF THE COMMONWEALTH PA $277,105
Gene Therapy 2018 NIDDK 5F30DK111145-02 Novel genetic engineering tools for functional studies of the gut microbiome CHEN, SWAY COLUMBIA UNIVERSITY HEALTH SCIENCES NY $42,966
Gene Therapy 2018 NHLBI 5R01HL122267-03 CF Gene Therapy with adeno-associated viral vectors CEBOTARU, LIUDMILA JOHNS HOPKINS UNIVERSITY MD $723,820
Gene Therapy 2018 NEI 5R01EY025752-02 Therapy development for open-angle glaucomas KOMAROMY, ANDRAS MICHIGAN STATE UNIVERSITY MI $691,835
Gene Therapy 2018 NHLBI 5R01HL129814-04 Calcium Pump Activators for Heart Failure Therapy THOMAS, DAVID UNIVERSITY OF MINNESOTA MN $805,140
Gene Therapy 2018 NHLBI 5R01HL130376-03 Final preclinical development of AAV gene therapy for atrial fibrillation DONAHUE, J UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $721,436
Gene Therapy 2018 NCI 5R01CA175386-05 Enhancing Therapy of Primary and Recurrent Tumors With Systemic Oncolytic Virus VILE, RICHARD MAYO CLINIC ROCHESTER MN $263,940
Gene Therapy 2018 NCI 5R01CA203873-03 A CEST-MRI Reporter Gene for Image Guided Oncolytic Virotherapy FARRAR, CHRISTIAN MASSACHUSETTS GENERAL HOSPITAL MA $391,481
Gene Therapy 2018 NCI 5R01CA178766-05 Creation of Immuno-Oncolytic Viruses for Cancer Therapy SARKAR, SAUMENDRA UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $319,550
Gene Therapy 2018 NCI 5R01CA186100-05 RNA Therapeutics for Targeted Treatment of Colon Cancer GUO, BIN UNIVERSITY OF HOUSTON TX $342,809
Gene Therapy 2018 NCI 5F30CA206296-03 Engineered Nanoparticles to Radioprotect Salivary Tissue VARGHESE, JOMY UNIVERSITY OF ROCHESTER NY $49,524
Gene Therapy 2018 NHLBI 5R00HL116234-05 Defining a therapeutic threshold in HSPC gene therapy for HIV-1 disease KIM, SANGGU OHIO STATE UNIVERSITY OH $249,000
Gene Therapy 2018 NHLBI 5R01HL097088-08 Next Generation of Recombinant AAV Serotype For Gene Therapy SRIVASTAVA, ARUN UNIVERSITY OF FLORIDA FL $770,648
Gene Therapy 2018 NHLBI 5P01HL131471-03 7022 Administrative Core FLOTTE, TERENCE UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $44,423
Gene Therapy 2018 NHLBI 5P01HL131471-03 7023 Viral Vector Core GAO, GUANG-PING UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $192,206
Gene Therapy 2018 NHLBI 5P01HL131471-03 7024 Animal Models Core MUELLER, CHRISTIAN UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $278,888
Gene Therapy 2018 NHLBI 5P01HL131471-03 7025 Respiratory Physiology Core ELMALLAH, MAI UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $205,875
Gene Therapy 2018 NHLBI 5P01HL131471-03 7026 Clinical Trial and Immunologic aspects of muscle-directed rAAV1-AAT gene therapy FLOTTE, TERENCE UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $477,375
Gene Therapy 2018 NHLBI 5P01HL131471-03 7027 Third generation liver-directed dual-function AAT vectors MUELLER, CHRISTIAN UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $670,000
Gene Therapy 2018 NHLBI 5P01HL131471-03 7028 Liver-directed somatic gene correction rAAV system of regulatable Cas9/sgRNA XUE, WEN UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $477,375
Gene Therapy 2018 NIGMS 5P30GM110787-05 6093 Genetic Technologies Core MENDENHALL, MICHAEL UNIVERSITY OF KENTUCKY KY $150,695
Gene Therapy 2018 NCI 5R01CA207240-02 Phase I trial of intravenous vesicular stomatitis virus for treatment of metastatic endometrial cancer BAKKUM-GAMEZ, JAMIE MAYO CLINIC ROCHESTER MN $543,708
Gene Therapy 2018 NHLBI 5R01HL131404-03 Anti-AAV Antibodies as an Obstacle to Cardiac AAV Gene Therapy HAJJAR, ROGER ICAHN SCHOOL OF MEDICINE AT MOUNT SINAI NY $821,439
Gene Therapy 2018 NIAID 5R01AI128201-02 Gene delivery for Anopheles mosquitoes RASGON, JASON PENNSYLVANIA STATE UNIVERSITY-UNIV PARK PA $381,889
Gene Therapy 2018 NHLBI 5R01HL125892-04 Targeted correction of the human CFTR gene EGAN, MARIE YALE UNIVERSITY CT $554,851
Gene Therapy 2018 NCATS 5R44TR001191-03 Phase 2: NIS proteins with altered anion specificity SUKSANPAISAN, LUKKANA IMANIS LIFE SCIENCES, LLC MN $733,941
Gene Therapy 2018 NIAAA 5R01AA024095-02 Gene Delivery of Neuroactive Steroids to Modulate Ethanol Reinforcement/Consumption MORROW, A UNIV OF NORTH CAROLINA CHAPEL HILL NC $400,240
Gene Therapy 2018 OD 5R24OD022005-03 A Comprehensive Human cDNA Library For Functional Gene Replacement in Drosophila BELLEN, HUGO BAYLOR COLLEGE OF MEDICINE TX $704,068
Gene Therapy 2018 NEI 5R01EY022975-05 Directed Evolution of Adeno-Associated Virus for Retinal Gene Therapy SCHAFFER, DAVID UNIVERSITY OF CALIFORNIA BERKELEY CA $337,048
Gene Therapy 2018 NCI 2P50CA100632-16 7427 Project 4: Off-the-shelf engineered cord blood-derived natural killer cells for the treatment acute lymphoblastic leukemia REZVANI, KATY UNIVERSITY OF TX MD ANDERSON CAN CTR TX $238,194
Gene Therapy 2018 NIAID 5R21AI133533-02 Nanoparticle Delivery of DNA Vaccine Against Zika Virus MAO, HAI-QUAN JOHNS HOPKINS UNIVERSITY MD $245,563
Gene Therapy 2018 NIDCD 5R01DC014160-05 Fetal Pharmacotherapy for Congenital Deafness BRIGANDE, JOHN OREGON HEALTH & SCIENCE UNIVERSITY OR $327,250
Gene Therapy 2018 NHLBI 5P01HL122173-04 8117 Administrative Services Core STORB, RAINER FRED HUTCHINSON CANCER RESEARCH CENTER WA $252,644
Gene Therapy 2018 NHLBI 5P01HL122173-04 8118 Core A: Immune Function Studies RAWLINGS, DAVID SEATTLE CHILDREN'S HOSPITAL WA $148,581
Gene Therapy 2018 NHLBI 5P01HL122173-04 8119 Core B: Biostatistics and Data Management STORER, BARRY FRED HUTCHINSON CANCER RESEARCH CENTER WA $194,196
Gene Therapy 2018 NHLBI 5P01HL122173-04 8120 Core C: Pharmaceutical Production PRESS, OLIVER FRED HUTCHINSON CANCER RESEARCH CENTER WA $398,666
Gene Therapy 2018 NHLBI 5P01HL122173-04 8121 Project 1: Cell Therapy for Correction of Blood Disorders STORB, RAINER FRED HUTCHINSON CANCER RESEARCH CENTER WA $464,475
Gene Therapy 2018 NHLBI 5P01HL122173-04 8122 Project 2: Minimal-Intensity Conditioning with Antibody-Targeted Alpha Radiation SANDMAIER, BRENDA FRED HUTCHINSON CANCER RESEARCH CENTER WA $487,791
Gene Therapy 2018 NHLBI 5P01HL122173-04 8123 Project 3: Gene Therapy for Correction of Blood Disorders KIEM, HANS-PETER FRED HUTCHINSON CANCER RESEARCH CENTER WA $607,654
Gene Therapy 2018 NCI 5R01CA196975-03 First in-human PET imaging studies of NIS reporter [18F]BF4 DEGRADO, TIMOTHY MAYO CLINIC ROCHESTER MN $172,718
Gene Therapy 2018 NCI 5R01CA197111-04 Immunotherapeutic Nanoparticle Delivery to Melanoma With MR-Guided Focused Ultrasound PRICE, RICHARD UNIVERSITY OF VIRGINIA VA $517,432
Gene Therapy 2018 NHLBI 5R01HL064274-17 Hepatic Gene Transfer for Treatment of Hemophilias A & B KAY, MARK STANFORD UNIVERSITY CA $555,896
Gene Therapy 2018 NCI 1P01CA225622-01 8112 Project 1: Targeting cytomegalovirus antigens in glioblastoma with regulatory T cell depletion SAMPSON, JOHN DUKE UNIVERSITY NC $532,398
Gene Therapy 2018 NCI 1P01CA225622-01 8116 Biostatistics and Bioinformatics Core HERNDON, JAMES DUKE UNIVERSITY NC $169,472
Gene Therapy 2018 NIDDK 5P30DK019525-42 7244 Viral Vector Core JOHNSTON, JULIE UNIVERSITY OF PENNSYLVANIA PA $28,011
Gene Therapy 2018 NCI 2P01CA018029-42A1 8718 Specific Adoptive Immunotherapy of AML with Engineered CD8+ T Cells GREENBERG, PHILIP FRED HUTCHINSON CANCER RESEARCH CENTER WA $838,209
Gene Therapy 2018 NCI 2P01CA018029-42A1 8719 BCMA Specific Chimeric Antigen Receptor (CAR)-T Cells for Treatment of Patients with Multiple Myeloma GREEN, DAMIAN FRED HUTCHINSON CANCER RESEARCH CENTER WA $796,412
Gene Therapy 2018 NIA 2P01AG031862-11 8865 Core B: High-Throughput Biology SCHULTZ, DAVID UNIVERSITY OF PENNSYLVANIA PA $220,421
Gene Therapy 2018 NCI 2P30CA033572-35 5256 GMP Manufacturing Core HORNE, DAVID BECKMAN RESEARCH INSTITUTE/CITY OF HOPE CA $129,478
Gene Therapy 2018 NCI 2P30CA033572-35 5262 Cancer Immunotherapeutics LEE, PETER BECKMAN RESEARCH INSTITUTE/CITY OF HOPE CA $45,501
Gene Therapy 2018 NCI 2P30CA033572-35 5263 Hematologic Malignancies FORMAN, STEPHEN BECKMAN RESEARCH INSTITUTE/CITY OF HOPE CA $42,489
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