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Funding


RCDC

Project Listing by Category


Back to Estimates of Funding for Various Research, Condition, and Disease Categories (RCDC) Click the column headings to sort project listings.
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CategoryFYFunding ICProject NumberSub Project #Project TitlePI NameOrg NameState / CountryAmount
Mucopolysaccharidoses (MPS) 2017 NIAID 1R21AI128087-01 Optimizing Gene Editing in Primary Human B Cells for Therapy and Research MORIARITY, BRANDEN UNIVERSITY OF MINNESOTA MN $228,750
Mucopolysaccharidoses (MPS) 2017 NINDS 5R01NS092671-02 Upregulation of Iduronidase Enzyme in MPSI Disease BROTHERS, SHAUN UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $335,781
Mucopolysaccharidoses (MPS) 2017 NINDS 5R01NS088766-03 Phenotypic effects of brain-directed enzyme therapy for Sanfilippo B syndrome DICKSON, PATRICIA LA BIOMED RES INST/ HARBOR UCLA MED CTR CA $310,283
Mucopolysaccharidoses (MPS) 2017 NICHD 5F30HD081853-03 Novel Dried Blood Spot Mass Spectrometry Functional Assays for Lysosomal Acid Lipase and N-acetylgalactosamine-sulfate Sulfatases for Use in Newborn Screening MASI, SOPHIA UNIVERSITY OF WASHINGTON WA $49,044
Mucopolysaccharidoses (MPS) 2017 NIDDK 5R01DK054481-21 Gene Therapy for Mucopolysaccharidosis CASAL, MARGRET UNIVERSITY OF PENNSYLVANIA PA $537,061
Mucopolysaccharidoses (MPS) 2017 NIAMS 1F32AR071298-01 Impaired BMP Signaling and Failed Bone Formation in Mucopolysaccharidosis VII PECK, SUN UNIVERSITY OF PENNSYLVANIA PA $65,250
Mucopolysaccharidoses (MPS) 2017 NINDS 5R42NS089061-03 Development and validation of therapy for mucopolysaccharidosis III EKINS, SEAN PHOENIX NEST, INC. NY $777,801
Mucopolysaccharidoses (MPS) 2017 NIDDK 5R01DK067859-17 Multiplex Analysis of Inborn Errors of Metabolism GELB, MICHAEL UNIVERSITY OF WASHINGTON WA $582,226
Mucopolysaccharidoses (MPS) 2017 NINDS 5R01NS085381-05 Neuroimaging and Neuropathology of Mucopolysaccharidosis I DICKSON, PATRICIA LA BIOMED RES INST/ HARBOR UCLA MED CTR CA $304,460
Mucopolysaccharidoses (MPS) 2017 NINDS 5R21NS096044-02 Modified neural stem cells for glycosylation-independent treatment of MPS IIIB IACOVINO, MICHELINA LA BIOMED RES INST/ HARBOR UCLA MED CTR CA $295,624
Mucopolysaccharidoses (MPS) 2017 NCATS 5U54NS065768-09 5620 Longitudinal Studies of Brain Structure and Function in MPS Disorders WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $44,995
Mucopolysaccharidoses (MPS) 2017 NIDDK 5U54NS065768-09 5620 Longitudinal Studies of Brain Structure and Function in MPS Disorders WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $71,244
Mucopolysaccharidoses (MPS) 2017 NINDS 5U54NS065768-09 5620 Longitudinal Studies of Brain Structure and Function in MPS Disorders WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $51,721
Mucopolysaccharidoses (MPS) 2017 NCATS 5U54NS065768-09 5622 Longitudinal Study of Bone and Endocrine Disease in Children with MPS I, II, and VI: A Multi-Center Study of the Lysosomal Disease Network POLGREEN, LYNDA UNIVERSITY OF MINNESOTA MN $25,720
Mucopolysaccharidoses (MPS) 2017 NIDDK 5U54NS065768-09 5622 Longitudinal Study of Bone and Endocrine Disease in Children with MPS I, II, and VI: A Multi-Center Study of the Lysosomal Disease Network POLGREEN, LYNDA UNIVERSITY OF MINNESOTA MN $40,725
Mucopolysaccharidoses (MPS) 2017 NINDS 5U54NS065768-09 5622 Longitudinal Study of Bone and Endocrine Disease in Children with MPS I, II, and VI: A Multi-Center Study of the Lysosomal Disease Network POLGREEN, LYNDA UNIVERSITY OF MINNESOTA MN $29,565
Mucopolysaccharidoses (MPS) 2017 NCATS 5U54NS065768-09 5624 An Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I CHEN, AGNES UNIVERSITY OF MINNESOTA MN $12,052
Mucopolysaccharidoses (MPS) 2017 NIDDK 5U54NS065768-09 5624 An Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I CHEN, AGNES UNIVERSITY OF MINNESOTA MN $19,084
Mucopolysaccharidoses (MPS) 2017 NINDS 5U54NS065768-09 5624 An Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I CHEN, AGNES UNIVERSITY OF MINNESOTA MN $13,854
Mucopolysaccharidoses (MPS) 2017 NCATS 5U54NS065768-09 5630 Natural History Study for MPS IMC and MPS MID LEVY, PAUL UNIVERSITY OF MINNESOTA MN $2,040
Mucopolysaccharidoses (MPS) 2017 NIDDK 5U54NS065768-09 5630 Natural History Study for MPS IMC and MPS MID LEVY, PAUL UNIVERSITY OF MINNESOTA MN $3,230
Mucopolysaccharidoses (MPS) 2017 NINDS 5U54NS065768-09 5630 Natural History Study for MPS IMC and MPS MID LEVY, PAUL UNIVERSITY OF MINNESOTA MN $2,345
Mucopolysaccharidoses (MPS) 2017 NICHD 1R41HD092110-01 Structure-based optimization of a novel pharmacological chaperone therapy for MPSIIIC EKINS, SEAN PHOENIX NEST, INC. NY $224,873
Mucopolysaccharidoses (MPS) 2017 NINDS 1R44NS102086-01 Improving MPS I ERT Efficacy through Lectin-Mediated Delivery RADIN, DAVID BIOSTRATEGIES, LC AR $1,237,037
Mucopolysaccharidoses (MPS) 2017 NIAMS 1R01AR071975-01 Pathogenesis and Treatment of Bone Disease in the Mucopolysaccharidoses SMITH, LACHLAN UNIVERSITY OF PENNSYLVANIA PA $363,084
Mucopolysaccharidoses (MPS) 2017 NINDS 1R01NS102624-01 Optimizing AAV Vectors for Central Nervous System transduction HELDERMON, COY UNIVERSITY OF FLORIDA FL $624,036
Mucopolysaccharidoses (MPS) 2017 NINDS 1K08NS102398-01 Correction of Mucopolysaccharidosis type 1: Targeting safe harbor loci using genome editing GOMEZ-OSPINA, NATALIA STANFORD UNIVERSITY CA $196,236
Mucopolysaccharidoses (MPS) 2017 NINDS 3R21NS096044-01S1 Modified neural stem cells for slycosylation-independent treatment of MPS IIIB IACOVINO, MICHELINA LA BIOMED RES INST/ HARBOR UCLA MED CTR CA $27,547
Mucopolysaccharidoses (MPS) 2017 NCATS 1R43TR002238-01 Novel nanoparticle-based enzyme replacement therapy for Hunter Syndrome IGNAR, DIANE NEURO10-9 PHARMA, INC. NC $223,671
Mucopolysaccharidoses (MPS) 2017 NCATS 3R01NS088766-03S1 Phenotypic effects of brain-directed enzyme therapy for Sanfilippo B syndrome DICKSON, PATRICIA LA BIOMED RES INST/ HARBOR UCLA MED CTR CA $100,000


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