Skip Navigation
 

Funding


RCDC

Project Listing by Category


Back to Estimates of Funding for Various Research, Condition, and Disease Categories (RCDC) Click the column headings to sort project listings.
  Help
123
CategoryFYFunding ICProject NumberSub Project #Project TitlePI NameOrg NameState / CountryAmount
Gene Therapy 2017 NIAMS 5R21AR066938-02 Human artificial chromosome as vectors for gene therapy of a model skin disease MONACO, ZOIA TUFTS UNIVERSITY MEDFORD MA $208,548
Gene Therapy 2017 NIAMS 5R01AR067707-02 In Vivo Gene Targeting to Treat Inherited Bone Disease DEYLE, DAVID MAYO CLINIC ROCHESTER MN $349,800
Gene Therapy 2017 NIAMS 5R21AR068040-02 First-in-Human rAAVrh74.MCK.GALGT2 DMD Clinical Trial FLANIGAN, KEVIN RESEARCH INST NATIONWIDE CHILDREN'S HOSP OH $263,120
Gene Therapy 2017 NCI 5F30CA180731-03 TCR Gene Transfer for Treating HCV-Associated Malignancies SPEAR, TIMOTHY LOYOLA UNIVERSITY CHICAGO IL $49,044
Gene Therapy 2017 NHLBI 5U01HL121842-02 Phase II Study of AAV9-GAA Gene Transfer in Pompe Disease BYRNE, BARRY UNIVERSITY OF FLORIDA FL $564,323
Gene Therapy 2017 NIAID 5R01AI097320-05 Pre-Clinical Development of Nuclease Mediated Gene Therapy for SCID PORTEUS, MATTHEW STANFORD UNIVERSITY CA $394,389
Gene Therapy 2017 NHLBI 5R42HL122038-03 Urocortin-2 Gene Transfer for CHF: a Paracrine Approach Using Intravenous AAV8 HAMMOND, H. KIRK RENOVA THERAPEUTICS, INC. CA $802,500
Gene Therapy 2017 NIGMS 5F32GM112337-02 Microtubule Motors in Axonal Sorting and Transport During Herpesvirus Infections SCHERER, JULIAN PRINCETON UNIVERSITY NJ $59,166
Gene Therapy 2017 NIAID 5R01AI051390-16 Immunology of factor IX gene transfer to liver HERZOG, ROLAND UNIVERSITY OF FLORIDA FL $337,500
Gene Therapy 2017 NCI 5P30CA014195-44 7749 PL Mouse HUNTER, TONY SALK INSTITUTE FOR BIOLOGICAL STUDIES CA $24,970
Gene Therapy 2017 NCI 5R01CA175052-04 Enhanced GBM Therapy Using a New Class of HSV Oncolytic Vector GLORIOSO, JOSEPH UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $316,018
Gene Therapy 2017 NCI 5P30CA014195-44 7759 SR Fun Gen HUNTER, TONY SALK INSTITUTE FOR BIOLOGICAL STUDIES CA $283,364
Gene Therapy 2017 NCI 5P30CA014195-44 7760 SR Gene Therapy HUNTER, TONY SALK INSTITUTE FOR BIOLOGICAL STUDIES CA $137,679
Gene Therapy 2017 NIDCD 5R00DC013555-04 Rescue of channelopathy induced anosmias MCINTYRE, JEREMY UNIVERSITY OF FLORIDA FL $248,999
Gene Therapy 2017 NCI 5R01CA166590-05 Cancer Prevention and Treatment by Activation of a Brain-Adipocyte Axis CAO, LEI OHIO STATE UNIVERSITY OH $319,550
Gene Therapy 2017 NCI 5R01CA077544-16 Control of CMV infection post-HCT using attenuated MVA-based CMV subunit vaccine DIAMOND, DON BECKMAN RESEARCH INSTITUTE/CITY OF HOPE CA $539,228
Gene Therapy 2017 NCI 5R01CA194064-03 Combination Therapy of OvCA with Oligonucleotides and Photodynamic Therapy MING, XIN WAKE FOREST UNIVERSITY HEALTH SCIENCES NC $283,650
Gene Therapy 2017 NHLBI 5R01HL125703-03 PET/MRI to study nanotherapy in atherosclerosis MULDER, WILLEM ICAHN SCHOOL OF MEDICINE AT MOUNT SINAI NY $590,721
Gene Therapy 2017 NCI 5R01CA168448-05 Next Generation Oncolytic Adenovirus for Advanced Pancreatic Cancer Treatment YAMAMOTO, MASATO UNIVERSITY OF MINNESOTA MN $315,400
Gene Therapy 2017 NINDS 5P30NS045776-13 7972 Core C Interdepartmental Neuroscience Center BREAKEFIELD, XANDRA MASSACHUSETTS GENERAL HOSPITAL MA $237,463
Gene Therapy 2017 NIAID 5R37AI091476-07 Therapeutic Use of an Enhanced Form of CD4-Ig FARZAN, MICHAEL SCRIPPS FLORIDA FL $951,702
Gene Therapy 2017 NIAID 5R01AI113221-03 Modulating Immunity to Nucleic Acids and Inducing Tolerance by Gene Transfer BROWN, BRIAN ICAHN SCHOOL OF MEDICINE AT MOUNT SINAI NY $421,004
Gene Therapy 2017 NIDA 5P30DA033934-04 6609 Mutant Mouse/Viral Vector LICHTMAN, ARON VIRGINIA COMMONWEALTH UNIVERSITY VA $142,738
Gene Therapy 2017 NHLBI 5R01HL089221-09 Determinants of AAV Tropism ASOKAN, ARAVIND UNIV OF NORTH CAROLINA CHAPEL HILL NC $448,381
Gene Therapy 2017 NIGMS 5R01GM108487-04 MuLV p12 function in tethering & integration ROTH, MONICA RBHS-ROBERT WOOD JOHNSON MEDICAL SCHOOL NJ $295,661
Gene Therapy 2017 NCI 5R01CA174861-04 Novel Theranostics for Pancreatic Cancer DAVYDOVA, JULIA UNIVERSITY OF MINNESOTA MN $319,031
Gene Therapy 2017 NCI 5R01CA195503-02 Nanoparticle modified Human Fat Derived Mesenchymal Stem Cells for Brain Cancer GREEN, JORDAN JOHNS HOPKINS UNIVERSITY MD $10,280
Gene Therapy 2017 NEI 5K08EY023993-04 Molecular Profiling of Rods to Identify New Therapies for Retinal Degenerations WU, DAVID MASSACHUSETTS EYE AND EAR INFIRMARY MA $222,047
Gene Therapy 2017 NEI 5K08EY026101-02 A nanoparticle platform for targeted delivery of therapeutic agents to retinal pigment epithelial or choroidal endothelial cells YIU, GLENN UNIVERSITY OF CALIFORNIA AT DAVIS CA $206,553
Gene Therapy 2017 NIDDK 5R01DK048252-23 Transgene Persistence in Liver Gene Therapy GROMPE, MARKUS OREGON HEALTH & SCIENCE UNIVERSITY OR $368,829
Gene Therapy 2017 NEI 5R01EY002422-36 Mechanisms and Therapeutic Treatments for Inherited Retinal Degenerative Diseases MOLDAY, ROBERT UNIVERSITY OF BRITISH COLUMBIA CANADA $267,961
Gene Therapy 2017 NCI 5R01CA200900-02 Systemic RNA Delivery to Tumors SHI, JINJUN BRIGHAM AND WOMEN'S HOSPITAL MA $547,422
Gene Therapy 2017 NIDDK 5P30DK041301-28 7944 Core D: Integrated Molecular Technologies KASAHARA, NORIYUKI UNIVERSITY OF CALIFORNIA LOS ANGELES CA $143,990
Gene Therapy 2017 NHLBI 5R01HL119046-04 Targeting Abnormal Calcium Cycling Using Novel Gene Therapy Vectors HAJJAR, ROGER ICAHN SCHOOL OF MEDICINE AT MOUNT SINAI NY $733,804
Gene Therapy 2017 NCI 5F30CA174058-05 Overcoming Temozolomide Resistance using MGMT-targeting Spherical Nucleic Acids SITA, TIMOTHY NORTHWESTERN UNIVERSITY IL $49,044
Gene Therapy 2017 NEI 5R01EY024958-03 CONVERTING BIPOLAR CELLS INTO RED-SHIFTED OPTOGENETIC SENSORS FOR RETINAL THERAPY CORBO, JOSEPH WASHINGTON UNIVERSITY MO $442,532
Gene Therapy 2017 NHLBI 5R01HL126850-02 Novel factor VIII variants for improved efficacy in gene therapy for hemophilia A SABATINO, DENISE CHILDREN'S HOSP OF PHILADELPHIA PA $420,000
Gene Therapy 2017 NEI 5R01EY013433-10 A Ribozyme Rescue Strategy for Autosomal Dominant Retinitis Pigmentosa SULLIVAN, JOHN STATE UNIVERSITY OF NEW YORK AT BUFFALO NY $378,000
Gene Therapy 2017 NHLBI 5R01HL086741-09 Genetic Engineering of Vein Bypass Grafts in Vascular and Cardiovascular Surgery LOGERFO, FRANK BETH ISRAEL DEACONESS MEDICAL CENTER MA $462,922
Gene Therapy 2017 NHLBI 5R01HL130871-02 Development of highly efficient factor VIII mini-gene therapy XIAO, WEIDONG TEMPLE UNIV OF THE COMMONWEALTH PA $487,271
Gene Therapy 2017 NHLBI 5R01HL120521-04 Cell-specific gene delivery methods for expression and silencing in the lung DEAN, DAVID UNIVERSITY OF ROCHESTER NY $383,750
Gene Therapy 2017 NCI 5R01CA196215-02 Systemic Therapy with Infectivity-Selective Oncolytic Adenovirus for PDAC YAMAMOTO, MASATO UNIVERSITY OF MINNESOTA MN $348,844
Gene Therapy 2017 NCI 5P01CA094237-15 7528 CELL AND VECTOR PRODUCTION HESLOP, HELEN BAYLOR COLLEGE OF MEDICINE TX $492,025
Gene Therapy 2017 NCI 5P01CA094237-15 7530 CHIMERIC T CELLS TARGETING NEUROBLASTOMA HESLOP, HELEN BAYLOR COLLEGE OF MEDICINE TX $295,506
Gene Therapy 2017 NIAID 5R01AI029329-27 Enhancing the Intracellular Functioning of anti-HV RNAS ROSSI, JOHN BECKMAN RESEARCH INSTITUTE/CITY OF HOPE CA $654,174
Gene Therapy 2017 NICHD 5U01HD079066-03 Choroid Plexus-Directed Gene Therapy for Alpha-Mannosidosis WOLFE, JOHN CHILDREN'S HOSP OF PHILADELPHIA PA $530,182
Gene Therapy 2017 NCI 5P30CA008748-51 7556 Gene Transfer RIVIERE, ISABELLE SLOAN-KETTERING INST CAN RESEARCH NY $386,610
Gene Therapy 2017 NINDS 5R01NS088667-03 Disseminated gene delivery to the CNS by human iPSC-derived neural stem cells WOLFE, JOHN CHILDREN'S HOSP OF PHILADELPHIA PA $367,500
Gene Therapy 2017 NIAMS 5R01AR044345-19 Genes and Therapies for Centronuclear Myopathies BEGGS, ALAN BOSTON CHILDREN'S HOSPITAL MA $369,750
Gene Therapy 2017 NIGMS 5R01GM105691-04 MegaTALS: hyperspecific reagents for targeted gene modification and correction STODDARD, BARRY FRED HUTCHINSON CANCER RESEARCH CENTER WA $334,400
Gene Therapy 2017 NHLBI 5R01HL131143-02 Development of a gene therapy approach to treat acute lung injury using a preclinical, large animal model DEAN, DAVID UNIVERSITY OF ROCHESTER NY $776,235
Gene Therapy 2017 NIAAA 5K01AA024174-02 Connective tissue growth factor: an intriguing therapeutic target in alcoholic liver disease PI, LIYA UNIVERSITY OF FLORIDA FL $145,057
Gene Therapy 2017 NICHD 5R01HD083680-03 Mechanisms of cognitive deficits in dystroglycanopathies HU, HUAIYU UPSTATE MEDICAL UNIVERSITY NY $563,377
Gene Therapy 2017 NIDDK 5R01DK102861-03 Translational study of miR-146a gene therapy for diabetic peripheral neuropathy LIU, XIANSHUANG HENRY FORD HEALTH SYSTEM MI $334,125
Gene Therapy 2017 NCI 5R01CA193140-02 Targeting the Ig-light chains with CAR-T cells in lymphoid tumors DOTTI, GIANPIETRO UNIV OF NORTH CAROLINA CHAPEL HILL NC $569,255
Gene Therapy 2017 NINDS 5R01NS086960-05 Targeted gene transfer across specific synapse types GELLER, ALFRED LSU HEALTH SCIENCES CENTER LA $319,375
Gene Therapy 2017 NIAID 5R01AI102672-05 Improved Foamy Virus Vectors for AIDS Gene Therapy TROBRIDGE, GRANT WASHINGTON STATE UNIVERSITY WA $370,977
Gene Therapy 2017 NIGMS 5R01GM108073-03 Pre-clinical studies of novel mitochondrial gene therapies PALLADINO, MICHAEL UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $286,938
Gene Therapy 2017 NHLBI 1R01HL134839-01 In Vivo RNA-Mediated Gene Editing of Hemophilia A WEISSMAN, DREW UNIVERSITY OF PENNSYLVANIA PA $761,424
Gene Therapy 2017 NIA 5R37AG008796-26 Slow Outward Currents and Learning In Aging Hippocampus DISTERHOFT, JOHN NORTHWESTERN UNIVERSITY AT CHICAGO IL $569,055
Gene Therapy 2017 NIGMS 1R01GM121612-01 Making Oligonucleotides Better Biopharmaceuticals by Steric Protection ZHANG, KE NORTHEASTERN UNIVERSITY MA $318,402
Gene Therapy 2017 NIDCD 5R01DC014496-02 Gene Therapy for Treating Human Genetic Deafness Tested in Animal Models LIN, XI EMORY UNIVERSITY GA $481,848
Gene Therapy 2017 NIA 1R01NS099371-01 CircRNAs and CNS Gene Transfer ASOKAN, ARAVIND UNIV OF NORTH CAROLINA CHAPEL HILL NC $398,672
Gene Therapy 2017 NEI 1R01EY027414-01 Intravenous MitoTargeted AAV9 Gene Therapy for Treatment of Visual Loss and Encephalopathy in Leigh Syndrome and NARP GUY, JOHN UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $383,750
Gene Therapy 2017 NIAID 1R01AI128074-01 Restoring Immune Tolerance in a Model of Multiple Sclerosis HOFFMAN, BRAD UNIVERSITY OF FLORIDA FL $381,250
Gene Therapy 2017 NIAID 1R21AI127381-01 Redirected T Cell Therapy to Cure Invasive Fungal Infections KONTOYIANNIS, DIMITRIOS UNIVERSITY OF TX MD ANDERSON CAN CTR TX $211,202
Gene Therapy 2017 NIGMS 5R01GM088351-07 The mechanism of Cas9/CRISPR-initiated genome modification in human somatic cells HENDRICKSON, ERIC UNIVERSITY OF MINNESOTA MN $283,657
Gene Therapy 2017 NINDS 5F32NS095515-02 Treatment of Peripheral Nervous System Dysfunction in Giant Axonal Neuropathy BAILEY, RACHEL UNIV OF NORTH CAROLINA CHAPEL HILL NC $57,066
Gene Therapy 2017 NIAID 5R01AI116698-03 Selection of New rAAV Vectors Using Replicating Viral Capsids Libraries KAY, MARK STANFORD UNIVERSITY CA $593,119
Gene Therapy 2017 NIAID 1R21AI128087-01 Optimizing Gene Editing in Primary Human B Cells for Therapy and Research MORIARITY, BRANDEN UNIVERSITY OF MINNESOTA MN $228,750
Gene Therapy 2017 NIDDK 5R01DK058702-15 Nonintegrating Lentiviral Vectors Towards Clinical Trials KAFRI, TAL UNIV OF NORTH CAROLINA CHAPEL HILL NC $380,000
Gene Therapy 2017 NHLBI 5R01HL127413-03 Biodegradable Mucus Penetrating DNA Nanoparticle for Gene Therapy of CF HANES, JUSTIN JOHNS HOPKINS UNIVERSITY MD $396,404
Gene Therapy 2017 NCI 5P01CA163205-05 7345 Development of a Novel Class of Highly Specific and Effective Oncolytic HSV Vect GLORIOSO, JOSEPH UNIVERSITY OF PITTSBURGH PA $369,444
Gene Therapy 2017 NCI 5P01CA163205-05 7347 The Tumor Microenvironmental Barrier to Effective Viral Oncolysis KAUR, BALVEEN OHIO STATE UNIVERSITY OH $255,024
Gene Therapy 2017 NCI 5P01CA163205-05 7348 NK Innate Immunity and Oncolytic Virus Therapy CALIGIURI, MICHAEL OHIO STATE UNIVERSITY OH $251,009
Gene Therapy 2017 NCI 5P01CA163205-05 7349 Administration and Biostatistics Core CHIOCCA, E. OHIO STATE UNIVERSITY OH $125,783
Gene Therapy 2017 NCI 5P01CA163205-05 7350 Pre-Clinical Vector Production Core GOINS, WILLIAM UNIVERSITY OF PITTSBURGH PA $175,549
Gene Therapy 2017 NCI 5P01CA163205-05 7351 Malignant Gliomas Biorepository Core NAKANO, ICHIRO OHIO STATE UNIVERSITY OH $142,311
Gene Therapy 2017 NIBIB 5R01EB017766-04 Histone targeted non-viral gene delivery to enhance bone repair SULLIVAN, MILLICENT UNIVERSITY OF DELAWARE DE $349,848
Gene Therapy 2017 NHLBI 5R01HL114832-05 Improving dystrophin gene therapy through understanding dystrobrevin function TOWNSEND, DEWAYNE UNIVERSITY OF MINNESOTA MN $373,127
Gene Therapy 2017 NIBIB 5R01EB018956-03 Thermal Assisted Gene Electro Transfer to the Skin HELLER, RICHARD OLD DOMINION UNIVERSITY VA $344,250
Gene Therapy 2017 NIAMS 5R01AR040864-28 Dystrophin Replacement CHAMBERLAIN, JEFFREY UNIVERSITY OF WASHINGTON WA $576,032
Gene Therapy 2017 NHLBI 5R33HL120760-04 Lipidomic Screening For Functional Surfactant Gene Mutations COLE, FRANCIS WASHINGTON UNIVERSITY MO $459,059
Gene Therapy 2017 NIAMS 5R21AR067985-02 R16/17-Independent nNOS Anchoring Mechanism DUAN, DONGSHENG UNIVERSITY OF MISSOURI-COLUMBIA MO $160,713
Gene Therapy 2017 NCI 1R21CA212731-01 Nanoneedle microrobots for single cancer cell manipulation and genome editing DAVIS, RONALD STANFORD UNIVERSITY CA $314,000
Gene Therapy 2017 NIDDK 1R01DK107739-01A1 Novel Therapeutic Approaches For Treatment of Intestinal Inflammation MERLIN, DIDIER GEORGIA STATE UNIVERSITY GA $340,875
Gene Therapy 2017 NIAID 5R01AI117408-02 Enhance AAV Liver Transduction with Capsid Immune Evasion LI, CHENGWEN UNIV OF NORTH CAROLINA CHAPEL HILL NC $380,000
Gene Therapy 2017 NCI 5R01CA190144-03 Liver Cancer Risk with rAAV Gene Therapy GROMPE, MARKUS OREGON HEALTH & SCIENCE UNIVERSITY OR $585,925
Gene Therapy 2017 NIDCR 5R01DE025681-02 Nanolipidoids-Conjugated MicroRNA Enhance Oral and Cranial Bone Regeneration CHEN, JAKE TUFTS UNIVERSITY BOSTON MA $330,000
Gene Therapy 2017 NIDDK 5P30DK017047-41 6592 Core A: Viral Vector and Transgenic Mouse Core BORNFELDT, KARIN UNIVERSITY OF WASHINGTON WA $183,108
Gene Therapy 2017 NIMH 5R01MH102144-04 Validation of the Rev-dependent vector for targeting SIV macrophage reservoirs WU, YUNTAO GEORGE MASON UNIVERSITY VA $652,436
Gene Therapy 2017 NCI 5P30AI028697-28 7321 Gene and Cellular Therapy Core AN, DONG SUNG UNIVERSITY OF CALIFORNIA LOS ANGELES CA $14,175
Gene Therapy 2017 NHLBI 5P30AI028697-28 7321 Gene and Cellular Therapy Core AN, DONG SUNG UNIVERSITY OF CALIFORNIA LOS ANGELES CA $10,148
Gene Therapy 2017 NIA 5P30AI028697-28 7321 Gene and Cellular Therapy Core AN, DONG SUNG UNIVERSITY OF CALIFORNIA LOS ANGELES CA $990
Gene Therapy 2017 NIAID 5P30AI028697-28 7321 Gene and Cellular Therapy Core AN, DONG SUNG UNIVERSITY OF CALIFORNIA LOS ANGELES CA $66,430
Gene Therapy 2017 NICHD 5P30AI028697-28 7321 Gene and Cellular Therapy Core AN, DONG SUNG UNIVERSITY OF CALIFORNIA LOS ANGELES CA $2,996
Gene Therapy 2017 NIDA 5P30AI028697-28 7321 Gene and Cellular Therapy Core AN, DONG SUNG UNIVERSITY OF CALIFORNIA LOS ANGELES CA $7,195
Gene Therapy 2017 NIDDK 5P30AI028697-28 7321 Gene and Cellular Therapy Core AN, DONG SUNG UNIVERSITY OF CALIFORNIA LOS ANGELES CA $2,714
Gene Therapy 2017 NIGMS 5P30AI028697-28 7321 Gene and Cellular Therapy Core AN, DONG SUNG UNIVERSITY OF CALIFORNIA LOS ANGELES CA $2,714
Gene Therapy 2017 NHLBI 5P01HL112761-05 7685 FIX GENE THERAPY AND ROLE OF AAV NAb SAMULSKI, RICHARD UNIV OF NORTH CAROLINA CHAPEL HILL NC $171,119
Gene Therapy 2017 NHLBI 5P01HL112761-05 7686 HUMANIZING AAV VECTORS FOR GENE THERAPY ASOKAN, ARAVIND UNIV OF NORTH CAROLINA CHAPEL HILL NC $164,905
Gene Therapy 2017 NHLBI 5P01HL112761-05 7687 INTRAARTICULAR AAV TO CIRCUMVENT SYSTEMIC NEUTRALIZATION MONAHAN, PAUL UNIV OF NORTH CAROLINA CHAPEL HILL NC $149,913
Gene Therapy 2017 NHLBI 5P01HL112761-05 7688 GENERATION OF A MODEL OF HEMOPHILIA B IN AAV RESISTANT PRIMATES SULLENGER, BRUCE UNIV OF NORTH CAROLINA CHAPEL HILL NC $186,218
Gene Therapy 2017 NHLBI 5P01HL112761-05 7690 VECTOR AND MOLECULAR BIOLOGY CORE GREIGER, JOSHUA UNIV OF NORTH CAROLINA CHAPEL HILL NC $132,461
Gene Therapy 2017 NHLBI 5P01HL112761-05 7691 ANIMAL MODELS CORE LI, CHENGWEN UNIV OF NORTH CAROLINA CHAPEL HILL NC $270,890
Gene Therapy 2017 NHLBI 5P01HL112761-05 5691 FIX GENE THERAPY AND ROLE OF AAV NAb SAMULSKI, RICHARD UNIV OF NORTH CAROLINA CHAPEL HILL NC $171,116
Gene Therapy 2017 NHLBI 5P01HL112761-05 5692 HUMANIZING AAV VECTORS FOR GENE THERAPY ASOKAN, ARAVIND UNIV OF NORTH CAROLINA CHAPEL HILL NC $164,903
Gene Therapy 2017 NHLBI 5P01HL112761-05 5693 INTRAARTICULAR AAV TO CIRCUMVENT SYSTEMIC NEUTRALIZATION MONAHAN, PAUL UNIV OF NORTH CAROLINA CHAPEL HILL NC $149,911
Gene Therapy 2017 NHLBI 5P01HL112761-05 5694 GENERATION OF A MODEL OF HEMOPHILIA B IN AAV RESISTANT PRIMATES SULLENGER, BRUCE UNIV OF NORTH CAROLINA CHAPEL HILL NC $186,216
Gene Therapy 2017 NHLBI 5P01HL112761-05 5696 VECTOR AND MOLECULAR BIOLOGY CORE GREIGER, JOSHUA UNIV OF NORTH CAROLINA CHAPEL HILL NC $132,460
Gene Therapy 2017 NHLBI 5P01HL112761-05 5697 ANIMAL MODELS CORE SUN, JUNJIANG UNIV OF NORTH CAROLINA CHAPEL HILL NC $270,889
Gene Therapy 2017 NCI 5K08CA169005-05 Glioma immunotherapy with strategies based on autonomous parvovirus MVMp PAGLINO, JUSTIN YALE UNIVERSITY CT $117,418
Gene Therapy 2017 NCI 5R01CA164333-05 TGFbeta Blockade in MART TCR-Engineered T Cell Melanoma Immunotherapy in Man KOYA, RICHARD ROSWELL PARK CANCER INSTITUTE CORP NY $352,335
Gene Therapy 2017 NINDS 5R01NS095817-02 Systemic gene therapy for glioblastoma ZHOU, JIANGBING YALE UNIVERSITY CT $364,219
Gene Therapy 2017 NHLBI 2R01HL021796-30 Mechanisms of Prosthetic Arterial Bypass Graft Failure LOGERFO, FRANK BETH ISRAEL DEACONESS MEDICAL CENTER MA $768,102
Gene Therapy 2017 NIAAA 5P60AA006420-34 7577 Viral Vector Core CONTET, CANDICE SCRIPPS RESEARCH INSTITUTE CA $137,135
Gene Therapy 2017 NIAMS 5R01AR069085-02 CRISPR/Cas9-Based Gene Editing for the Correction of Duchenne Muscular Dystrophy GERSBACH, CHARLES DUKE UNIVERSITY NC $339,448
Gene Therapy 2017 NHLBI 5R01HL122332-03 Therapeutic potential for AAV/micro-dystrophin transfer to cardiopulmonary tissue CHAMBERLAIN, JEFFREY UNIVERSITY OF WASHINGTON WA $503,928
Gene Therapy 2017 NHLBI 1R01HL131814-01A1 Novel strategy for Enhancing miRNA as a Therapeutic for Cardiac Regeneration DZAU, VICTOR DUKE UNIVERSITY NC $397,500
Gene Therapy 2017 NIAAA 1R01AA024095-01A1 Gene Delivery of Neuroactive Steroids to Modulate Ethanol Reinforcement/Consumption MORROW, A UNIV OF NORTH CAROLINA CHAPEL HILL NC $398,739
Gene Therapy 2017 NIAMS 2R01AR057076-06A1 Regional Gene Therapy to Enhance Bone Repair LIEBERMAN, JAY UNIVERSITY OF SOUTHERN CALIFORNIA CA $604,757
Gene Therapy 2017 NIAID 5R03AI122040-02 Gene Therapy for the Treatment of Hereditary Angioedema PAGOVICH, ODELYA WEILL MEDICAL COLL OF CORNELL UNIV NY $84,750
Gene Therapy 2017 NIAMS 5R01AR067247-02 Collagen turnover-stimulated gene delivery to enhance chronic wound repair SULLIVAN, MILLICENT UNIVERSITY OF DELAWARE DE $344,097
Gene Therapy 2017 NIDDK 5K08DK107864-02 Acute inhibition of renal gene expression to prevent nephrotoxicity. EADON, MICHAEL INDIANA UNIV-PURDUE UNIV AT INDIANAPOLIS IN $156,891
Gene Therapy 2017 NEI 1R01EY025752-01A1 Therapy development for open-angle glaucomas KOMAROMY, ANDRAS MICHIGAN STATE UNIVERSITY MI $696,882
Gene Therapy 2017 NIGMS 1R01GM119186-01A1 Mechanism of high-efficiency transduction of hepatocytes by optimized AAV vectors ASLANIDI, GEORGE UNIVERSITY OF FLORIDA FL $293,563
Gene Therapy 2017 NIAID 9R01AI129582-04A1 Elucidate and Modulate Cell Signaling in NK Cells for Glioma Treatment YU, JIANHUA OHIO STATE UNIVERSITY OH $387,500
Gene Therapy 2017 NINDS 5R01NS093941-02 Whole-body therapy for GM2 gangliosidoses MARTIN, DOUGLAS AUBURN UNIVERSITY AT AUBURN AL $599,714
Gene Therapy 2017 NICHD 1R01HD090657-01 Placental-specific therapy for fetal growth restriction JONES, HELEN CINCINNATI CHILDRENS HOSP MED CTR OH $327,455
Gene Therapy 2017 NINDS 1K08NS096219-01A1 Global AAV gene therapy of Tay-Sachs disease in sheep. EDWARDS, HEATHER AUBURN UNIVERSITY AT AUBURN AL $169,128
Gene Therapy 2017 NCI 5R01CA183040-04 Ovarian cancer gene therapy using HPV pseudovirion WU, TZYY-CHOOU JOHNS HOPKINS UNIVERSITY MD $336,150
Gene Therapy 2017 NIDDK 5R01DK090058-07 Lentiviral-transduced hematopoictic stem cell transplantation for cystinosis CHERQUI, STEPHANIE UNIVERSITY OF CALIFORNIA SAN DIEGO CA $348,750
Gene Therapy 2017 NIAID 1R21AI121993-01A1 Multifactor mRNA Mediated T Cell Reprogramming for Systemic Lupus Erythematosus KATZ, SAMUEL YALE UNIVERSITY CT $293,125
Gene Therapy 2017 NIAID 1R21AI123896-01A1 Genome Editing to rescue FOXP3 Deficiency in IPEX syndrome BACCHETTA, ROSA STANFORD UNIVERSITY CA $199,558
Gene Therapy 2017 NIAMS 5R01AR063070-05 Skin-targeted Cell Therapy for Recessive Dystrophic Epidermolysis Bullosa TOLAR, JAKUB UNIVERSITY OF MINNESOTA MN $435,018
Gene Therapy 2017 NEI 5R01EY026682-02 Mechanistic Studies on Regenerative Medicine Approaches to Childhood Blindness BASSUK, ALEXANDER UNIVERSITY OF IOWA IA $389,825
Gene Therapy 2017 NEI 5R01EY008123-29 Photoreceptor Ciliopathies: UNC119 Paralogs and NPHP10/NPHP5 BAEHR, WOLFGANG UNIVERSITY OF UTAH UT $372,500
Gene Therapy 2017 NIAID 5R21AI117459-02 Novel DC targeted adenovirus vector for malaria vaccine development MORENO, ALBERTO EMORY UNIVERSITY GA $214,025
Gene Therapy 2017 NCI 5R01CA178766-04 Creation of Immuno-Oncolytic Viruses for Cancer Therapy SARKAR, SAUMENDRA UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $319,550
Gene Therapy 2017 NIDA 5R01DA034749-04 Neuropathic mechanisms and gene therapy on opioid dependence HAO, SHUANGLIN UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $345,449
Gene Therapy 2017 NIAID 5R01AI065429-13 Innate immunity to adenovirus SHAYAKHMETOV, DMITRY EMORY UNIVERSITY GA $390,000
Gene Therapy 2017 NCI 5R01CA167535-05 Novel Nanoparticle Therapy for Pancreatic Cancer MATTERS, GAIL PENNSYLVANIA STATE UNIV HERSHEY MED CTR PA $313,134
Gene Therapy 2017 NIDDK 5R01DK054481-21 Gene Therapy for Mucopolysaccharidosis CASAL, MARGRET UNIVERSITY OF PENNSYLVANIA PA $537,061
Gene Therapy 2017 NCI 5R01CA175318-03 A Nanotechnology Platform for Suicide Gene Therapy of Recurring Ovarian Cancer HATEFI, ARASH RUTGERS, THE STATE UNIV OF N.J. NJ $354,563
Gene Therapy 2017 NCI 5R01CA186730-03 Efficient Delivery of Plasmid DNA to Achieve Appropriate Transgene Expression HELLER, RICHARD OLD DOMINION UNIVERSITY VA $353,892
Gene Therapy 2017 NEI 5R01EY026564-02 Targeting Retinitis Pigmentosa Using Nanoparticle-Mediated Delivery of Genomic DNA HAN, ZONGCHAO UNIV OF NORTH CAROLINA CHAPEL HILL NC $374,323
Gene Therapy 2017 NHLBI 5R01HL116455-04 A Bioengineering Approach to Gene Therapy for Peripheral Arterial Disease ANNEX, BRIAN UNIVERSITY OF VIRGINIA VA $691,315
Gene Therapy 2017 NIAID 5U19AI117941-03 5327 Viral Immunology Core YANG, OTTO UNIVERSITY OF CALIFORNIA LOS ANGELES CA $207,272
Gene Therapy 2017 NIAID 5U19AI117941-03 5328 Improve the engraftment of combinatorial anti-HIV-1 gene modified HSPC AN, DONG SUNG UNIVERSITY OF CALIFORNIA LOS ANGELES CA $384,429
Gene Therapy 2017 NIAID 5U19AI117941-03 5329 Tracking the clonal behavior of repopulating cells CHEN, IRVIN UNIVERSITY OF CALIFORNIA LOS ANGELES CA $488,723
Gene Therapy 2017 NIAID 5U19AI117941-03 5330 Characterization of CAR-directed T-cells to suppress HIV-1 in vivo KITCHEN, SCOTT UNIVERSITY OF CALIFORNIA LOS ANGELES CA $676,680
Gene Therapy 2017 NIAID 5U19AI117941-03 5331 Pre-clinical development of gene modified stem cells and CAR T-cells for HIV-1 SYMONDS, GEOFFREY CALIMMUNE, INC. AZ $241,842
Gene Therapy 2017 NCI 5R01CA187923-03 Novel Strategies to Potentiate a Ras-targeted Oncolytic Herpes Simplex Virus ZHANG, XIAOLIU UNIVERSITY OF HOUSTON TX $344,023
Gene Therapy 2017 NEI 5R01EY025287-02 Plasticity of the human visual system studied in response to retinal gene therapy ASHTARI, MANZAR UNIVERSITY OF PENNSYLVANIA PA $541,647
Gene Therapy 2017 NIDDK 5P30DK054759-18 7716 Vector Core MCCRAY, PAUL UNIVERSITY OF IOWA IA $168,188
Gene Therapy 2017 NIAMS 5R01AR067491-03 Inhibition of NF-kB with siRNA/Peptide Nanoparticles for Arthritis Treatment PHAM, CHRISTINE WASHINGTON UNIVERSITY MO $362,701
Gene Therapy 2017 NIAID 5P01AI110485-03 5343 Safety and Durability of Integrase Defective Lentiviral vector for an HIV Vaccine KLOTMAN, MARY DUKE UNIVERSITY NC $615,983
Gene Therapy 2017 NCI 5R01CA056821-23 Immunization Against Melanoma Differentiation Antigens WOLCHOK, JEDD SLOAN-KETTERING INST CAN RESEARCH NY $299,950
Gene Therapy 2017 NIMH 5R01MH106460-02 Selective HDAC inhibition and therapeutic target genes: Identification of novel treatments for Bipolar Disorder MCCLUNG, COLLEEN UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $381,256
Gene Therapy 2017 NCI 5P30CA086862-17 7658 Cluster A: 2 Viral Vector Core SINN, PATRICK UNIVERSITY OF IOWA IA $58,111
Gene Therapy 2017 NHLBI 5R01HL097088-07 Next Generation of Recombinant AAV Serotype For Gene Therapy HERZOG, ROLAND UNIVERSITY OF FLORIDA FL $788,573
Gene Therapy 2017 NHLBI 5R01HL102035-08 Platelet-derived FVIII Gene Therapy of Hemophilia A SHI, QIZHEN MEDICAL COLLEGE OF WISCONSIN WI $367,344
Gene Therapy 2017 NINDS 5P01NS055976-10 7966 Cellular and Molecular Biology HOULE, JOHN DREXEL UNIVERSITY PA $70,845
Gene Therapy 2017 NINDS 5R01NS079568-05 Gene delivery to muscle and nerve for laminin-alpha2-deficient MD (MDC1A) XIAO, XIAO UNIV OF NORTH CAROLINA CHAPEL HILL NC $332,500
Gene Therapy 2017 NINDS 5R01NS087175-04 Giant Axonal Neuropathy Gene Therapy GRAY, STEVEN UNIV OF NORTH CAROLINA CHAPEL HILL NC $328,860
Gene Therapy 2017 NCATS 1R43TR001897-01 Enhancing CRISPR-based Therapeutic Interventions Via a Targeted Platform Tool LAPPI, DOUGLAS ADVANCED TARGETING SYSTEMS, INC. CA $150,000
Gene Therapy 2017 NINDS 5R01NS021328-33 Mitochondrial Inborn Errors in Metabolism WALLACE, DOUGLAS CHILDREN'S HOSP OF PHILADELPHIA PA $488,186
Gene Therapy 2017 NINDS 5F31NS096841-02 Cell-specific expression of AAV-Nurr1 in a model of Parkinson's Disease HAMMOND, SEAN COLORADO STATE UNIVERSITY CO $35,450
Gene Therapy 2017 NIDDK 5R01DK102767-03 Low Electric Field-Based Gene Delivery of IL-30 Gene Therapy for Liver Injury LI, SHULIN UNIVERSITY OF TX MD ANDERSON CAN CTR TX $360,000
Gene Therapy 2017 NEI 5U10EY024247-04 Biostatistics Center for Leber's Hereditary Optic Neuropathy: Gene Therapy Trial FEUER, WILLIAM UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $116,126
Gene Therapy 2017 NHLBI 1R43HL135969-01 Preclinical Evaluation of Ancestral Coagulation Factor VIII DENNING, GABRIELA EXPRESSION THERAPEUTICS GA $224,976
Gene Therapy 2017 NIAID 1R43AI125043-01A1 Screening for rAAV transduction enhancers BOWLIN, TERRY MICROBIOTIX, INC MA $299,999
Gene Therapy 2017 NCATS 1R42TR001711-01A1 A nanoparticle delivery system for CRISPR/Cas9 based therapeutics MA, PETER ATGC, INC. MI $225,000
Gene Therapy 2017 NIMH 1R43MH110273-01A1 Optogenetic control over transgene expression for the therapy of brain and spine MYAKISHEV-REMPEL, MAX LOCALIZED THERAPEUTICS, LLC NY $220,083
Gene Therapy 2017 NHLBI 1R01HL132840-01A1 Genetic Repair of Familial Hypercholesterolemia LAGOR, WILLIAM BAYLOR COLLEGE OF MEDICINE TX $596,073
Gene Therapy 2017 NCATS 1R43TR001904-01 Biomaterials for mRNA-based cellular reprogramming LEBAKKEN, CONNIE STEM PHARM, INC. WI $290,999
Gene Therapy 2017 NEI 1R41EY027667-01 Developing a new therapeutic agent for retinal ciliopathies KATSANIS, NICHOLAS RESCINDO THERAPEUTICS, INC. NC $238,837
Gene Therapy 2017 NINDS 5R01NS086352-04 PGC-1alpha and Pitx3 as individual and combined targets for neuroprotection SIMON, DAVID BETH ISRAEL DEACONESS MEDICAL CENTER MA $379,991
Gene Therapy 2017 NIAID 5U19AI117950-03 5399 Sequencing and Viral Evolution Core BUSHMAN, FREDERIC UNIVERSITY OF PENNSYLVANIA PA $271,334
Gene Therapy 2017 NIAID 5U19AI117950-03 5400 A PHASE I STUDY OF C34-CXCR4 MODIFIED CD4 T CELLS IN HIV-1 INFECTED INDIVIDUALS TEBAS, PABLO UNIVERSITY OF PENNSYLVANIA PA $678,794
Gene Therapy 2017 NIAID 5U19AI117950-03 5403 Programming Long Term Durable HIV-1 Specific T cell Responses WHERRY, E. UNIVERSITY OF PENNSYLVANIA PA $531,886
Gene Therapy 2017 NCI 1F31CA213668-01 CD40L-Modified Chimeric Antigen Receptor (CAR) T Cells KUHN, NICHOLAS SLOAN-KETTERING INST CAN RESEARCH NY $44,044
Gene Therapy 2017 NIBIB 1F31EB023090-01A1 Neurotrophic Nanoparticle Delivery with MRI-Guided Focused Ultrasound MEAD, BRIAN UNIVERSITY OF VIRGINIA VA $32,072
Gene Therapy 2017 NHLBI 5R21HL127495-02 Engineered CARs Targeting FVIII-specific T and B Cells SCOTT, DAVID HENRY M. JACKSON FDN FOR THE ADV MIL/MED MD $192,821
Gene Therapy 2017 NHLBI 5R01HL128139-03 Development of clinically feasible Ultrasound-mediated gene therapy for hemophilia MIAO, CAROL SEATTLE CHILDREN'S HOSPITAL WA $462,899
Gene Therapy 2017 NINDS 5R01NS088399-04 AAV capsid functions, immune evasion and neuronal targeting in mice and NHP NAKAI, HIROYUKI OREGON HEALTH & SCIENCE UNIVERSITY OR $336,875
Gene Therapy 2017 NIBIB 1F32EB023101-01A1 Sequence- and Stereocontrolled Triazolium-containing Precise Polymers for siRNA Complexation and Delivery GOLDER, MATTHEW MASSACHUSETTS INSTITUTE OF TECHNOLOGY MA $56,694
Gene Therapy 2017 NIAID 1F32AI126943-01A1 Allograft rejection and salvage therapy with chimeric antigen receptor T-regulatory cells in murine hindlimb transplant CONKLING, NICOLE UNIVERSITY OF CALIFORNIA, SAN FRANCISCO CA $62,922
Gene Therapy 2017 NIAMS 1F32AR071233-01 Genetic modification of immune cells to improve muscle regeneration RAMOS, JULIAN UNIVERSITY OF CALIFORNIA LOS ANGELES CA $57,066
Gene Therapy 2017 NCI 5R01CA196975-02 First in-human PET imaging studies of NIS reporter [18F]BF4 DEGRADO, TIMOTHY MAYO CLINIC ROCHESTER MN $189,087
Gene Therapy 2017 NHLBI 5R01HL118342-04 Macrophage Based Gene Therapy for Hereditary Pulmonary Alveolar Proteinosis TRAPNELL, BRUCE CINCINNATI CHILDRENS HOSP MED CTR OH $554,394
Gene Therapy 2017 NCI 5R01CA204968-02 Targeted Delivery of Brain Penetrating DNA Nanoparticles to Brain Tumors HANES, JUSTIN JOHNS HOPKINS UNIVERSITY MD $512,053
Gene Therapy 2017 NIDDK 5R01DK055759-18 AAV-Mediated Gene Targeting RUSSELL, DAVID UNIVERSITY OF WASHINGTON WA $336,038
Gene Therapy 2017 NEI 5U10EY023558-04 Leber's Hereditary Optic Neuropathy: Gene Therapy Clinical Trial GUY, JOHN UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $1,160,639
Gene Therapy 2017 NHLBI 1R01HL136135-01 Novel Gene Editing Approaches for Hemoglobinopathies KIEM, HANS-PETER FRED HUTCHINSON CANCER RESEARCH CENTER WA $959,786
Gene Therapy 2017 NHLBI 5U19HL129902-03 5442 NHP Model and Transplantation Core HU, SHIU-LOK UNIVERSITY OF WASHINGTON WA $485,926
Gene Therapy 2017 NHLBI 5U19HL129902-03 5443 Integrated Functional Genomics SEKALY, RAFICK-PIERRE CASE WESTERN RESERVE UNIVERSITY OH $236,571
Gene Therapy 2017 NHLBI 5U19HL129902-03 5444 Defining HIV sanctuary sites during autologous and allogeneic transplantation KEAN, LESLIE SEATTLE CHILDREN'S HOSPITAL WA $894,352
Gene Therapy 2017 NHLBI 5U19HL129902-03 5446 Overcoming barriers to efficient genome editing in HSPCs GREGORY, PHILIP SANGAMO BIOSCIENCES, INC. CA $198,489
Gene Therapy 2017 NHLBI 5U19HL129902-03 5447 Stem cell expansion and gene editing in a nonhuman primate model of HIV/AIDS KIEM, HANS-PETER FRED HUTCHINSON CANCER RESEARCH CENTER WA $530,022
Gene Therapy 2017 NCI 5R01CA196947-02 Disrupting tumor/bone malignant interactions with multifunctional cytokine sonodelivery FIGUEIREDO, MARXA PURDUE UNIVERSITY IN $350,644
Gene Therapy 2017 NICHD 5K08HD077040-05 Novel Approaches for Correcting Respiratory Insufficiency in Pompe Disease ELMALLAH, MAI UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $162,136
Gene Therapy 2017 NICHD 1R01HD088033-01A1 Optimizing Therapeutic delivery of MicroRNAs to prevent chronic lung disease in Preterm infants. ROGERS, LYNETTE RESEARCH INST NATIONWIDE CHILDREN'S HOSP OH $329,606
Gene Therapy 2017 NHLBI 5R00HL116234-04 Defining a therapeutic threshold in HSPC gene therapy for HIV-1 disease KIM, SANGGU OHIO STATE UNIVERSITY OH $249,000
Gene Therapy 2017 NHLBI 5P01HL091799-09 7161 Gene Vector Core RABIONOWITZ, JOSEPH TEMPLE UNIV OF THE COMMONWEALTH PA $277,107
Gene Therapy 2017 NINDS 5R01NS064404-08 Ultrasound-aided gene transfer to direct cortical neurogenesis after brain injury PUN, SUZIE UNIVERSITY OF WASHINGTON WA $435,092
Gene Therapy 2017 NIAID 5R01AI071068-12 Acute/chronic limitations to transcriptional RNAi therapies for infectious and other liver diseases KAY, MARK STANFORD UNIVERSITY CA $481,343
Gene Therapy 2017 NHLBI 5R01HL125030-04 Survival of the fittest HSPC repopulating clones by anti-HIV-1 gene-modification CHEN, IRVIN UNIVERSITY OF CALIFORNIA LOS ANGELES CA $385,000
Gene Therapy 2017 NEI 5R24EY022023-05 rAAV-CNGB3 Gene Therapy for Achromatopsia: Translational Research Studies HAUSWIRTH, WILLIAM UNIVERSITY OF FLORIDA FL $1,613,805
Gene Therapy 2017 NCI 5R01CA203852-02 Reconstruction of an oncolytic HSV vector for systemic delivery ZHANG, XIAOLIU UNIVERSITY OF HOUSTON TX $344,205
Gene Therapy 2017 NIBIB 5R01EB022148-02 Cancer-specific nanoparticle-mediated gene therapy to treat hepatocellular carcinoma GREEN, JORDAN JOHNS HOPKINS UNIVERSITY MD $364,500
Gene Therapy 2017 NIAID 5R01AI072176-10 Rational and Combinatorial Engineering of AAV Vectors HIRSCH, MATTHEW UNIV OF NORTH CAROLINA CHAPEL HILL NC $378,128
Gene Therapy 2017 OD 5U01AI107355-05 CCL1 gene therapy to inhibit bacterial translocation in acute radiation syndromes SUZUKI, FUJIO UNIVERSITY OF TEXAS MED BR GALVESTON TX $509,429
Gene Therapy 2017 NIBIB 5R03EB022155-02 Creating a Localized Pool of iPSCs In Vivo COOPER, GREGORY UNIVERSITY OF PITTSBURGH AT PITTSBURGH PA $77,625
Gene Therapy 2017 NINDS 5R01NS088689-04 Silencing C9or72 with rAAV Mediated RNAi BROWN, ROBERT UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $464,134
Gene Therapy 2017 NCI 5R01CA197111-03 Immunotherapeutic Nanoparticle Delivery to Melanoma With MR-Guided Focused Ultrasound PRICE, RICHARD UNIVERSITY OF VIRGINIA VA $519,263
Gene Therapy 2017 NHLBI 5R01HL129814-03 Calcium Pump Activators for Heart Failure Therapy THOMAS, DAVID UNIVERSITY OF MINNESOTA MN $795,914
Gene Therapy 2017 NINDS 5R01NS083848-05 Development of novel transsynaptic tracers for use in the central nervous system CEPKO, CONSTANCE HARVARD MEDICAL SCHOOL MA $365,020
Gene Therapy 2017 NINDS 5R01NS082289-05 Development of Intravenous AAV Vectors for Intractable Epilepsy MCCOWN, THOMAS UNIV OF NORTH CAROLINA CHAPEL HILL NC $332,500
Gene Therapy 2017 NIDDK 5F31DK108624-02 Hemophilia B Gene Therapy via CRISPR/Cas9-Targeted Integration of the Factor IX Gene using Adenovirus Vector Delivery STEPHENS, CALVIN WASHINGTON UNIVERSITY MO $30,651
Gene Therapy 2017 NCI 5R01CA172713-05 PATTERNS OF r AAV VECTOR INSERTION ASSOCIATED WITH LIVER TUMORS IN A MOUSE MODEL FU, HAIYAN RESEARCH INST NATIONWIDE CHILDREN'S HOSP OH $303,988
Gene Therapy 2017 NHLBI 5R01HL123326-02 Direct in vivo bone marrow transfer of lentiviral vector to correct hemophilia A MIAO, CAROL SEATTLE CHILDREN'S HOSPITAL WA $482,250
Gene Therapy 2017 NCI 5R01CA203873-02 A CEST-MRI Reporter Gene for Image Guided Oncolytic Virotherapy FARRAR, CHRISTIAN MASSACHUSETTS GENERAL HOSPITAL MA $406,309
Gene Therapy 2017 NIAID 2R01AI098446-05 Immunoglobulins Delivered by AVV Vector for the Prevention of SIV Infection DESROSIERS, RONALD UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $731,021
Gene Therapy 2017 NCI 5U01CA183012-04 Stem Cell Gene Therapy Following R-EPOCH for Non-Hodgkin Lymphoma in AIDS Patient ZAIA, JOHN BECKMAN RESEARCH INSTITUTE/CITY OF HOPE CA $312,304
Gene Therapy 2017 NIA 5R01NS094595-02 Effects of modified erythropoietin on cognition and neuropathology MCDONALD, MICHAEL UNIVERSITY OF TENNESSEE HEALTH SCI CTR TN $48,006
Gene Therapy 2017 NINDS 5R01NS094595-02 Effects of modified erythropoietin on cognition and neuropathology MCDONALD, MICHAEL UNIVERSITY OF TENNESSEE HEALTH SCI CTR TN $336,040
Gene Therapy 2017 NIDDK 5P30DK047757-23 7825 Core A - Vector Core JOHNSTON, JULIE UNIVERSITY OF PENNSYLVANIA PA $302,451
Gene Therapy 2017 NIDDK 5P30DK047757-23 7826 Core B - Immunology Core CALCEDO, ROBERTO UNIVERSITY OF PENNSYLVANIA PA $158,801
Gene Therapy 2017 NIBIB 5R01EB009903-08 Cytoplasmic trafficking of non-viral gene therapy vectors DEAN, DAVID UNIVERSITY OF ROCHESTER NY $345,375
Gene Therapy 2017 NIGMS 5R01GM115911-02 Engineered Cas9 Nucleases with Single-Genomic-Site Precision for CYBB Correction WOLFE, SCOT UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $388,765
Gene Therapy 2017 NHLBI 5R01HL125892-03 Targeted correction of the human CFTR gene EGAN, MARIE YALE UNIVERSITY CT $554,851
Gene Therapy 2017 NIGMS 5F31GM119392-02 Tailoring liposomal spherical nucleic acid nanoparticles for biological and therapeutic potency FERRER, JENNIFER NORTHWESTERN UNIVERSITY IL $38,012
Gene Therapy 2017 NCI 5R01CA177932-05 Design of Oncolytic Adenovirus Conjugated with Novel Polymer for Cancer Treatment KIM, SUNG WAN UNIVERSITY OF UTAH UT $309,175
Gene Therapy 2017 NHLBI 5R01HL116217-05 Engraftment and in vivo selection of HIV-protected stem cells KIEM, HANS-PETER FRED HUTCHINSON CANCER RESEARCH CENTER WA $523,418
Gene Therapy 2017 NHLBI 5R01HL122267-02 CF Gene Therapy with adeno-associated viral vectors CEBOTARU, LIUDMILA JOHNS HOPKINS UNIVERSITY MD $664,618
Gene Therapy 2017 NINDS 5R21NS098131-02 Gene Therapy for Upper Airway and Respiratory Insufficiency in an ALS Mouse Model ELMALLAH, MAI UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $209,375
Gene Therapy 2017 NIAAA 5R01AA024757-02 GDNF gene therapy to block relapse of heavy alcohol use in monkeys FORD, MATTHEW OREGON HEALTH & SCIENCE UNIVERSITY OR $519,051
Gene Therapy 2017 NCI 5R21CA193055-03 In situ Imaging of CAR T-cells WILLIAMS, JOHN BECKMAN RESEARCH INSTITUTE/CITY OF HOPE CA $258,825
Gene Therapy 2017 NCI 5F30CA206296-02 Engineered Nanoparticles to Radioprotect Salivary Tissue VARGHESE, JOMY UNIVERSITY OF ROCHESTER NY $49,044
Gene Therapy 2017 NIDCD 5R01DC014160-04 Fetal Pharmacotherapy for Congenital Deafness BRIGANDE, JOHN OREGON HEALTH & SCIENCE UNIVERSITY OR $327,250
Gene Therapy 2017 NINDS 5R21NS098497-02 A new approach to modeling ALS based on TBK1 mutation in mice XU, ZUOSHANG UNIV OF MASSACHUSETTS MED SCH WORCESTER MA $209,375
Gene Therapy 2017 NINDS 5R21NS098137-02 Development of DNAzyme Gene Therapy for Huntington's Disease REINER, ANTON UNIVERSITY OF TENNESSEE HEALTH SCI CTR TN $228,000
Gene Therapy 2017 NEI 5R01EY024280-04 Developing efficient AAV vectors for photoreceptor targeting via the vitreous BOYE, SHANNON UNIVERSITY OF FLORIDA FL $472,914
Gene Therapy 2017 NEI 5R01EY017294-10 Gene Therapy in the Cornea MOHAN, RAJIV UNIVERSITY OF MISSOURI-COLUMBIA MO $379,665
Gene Therapy 2017 NHLBI 5R01HL064274-16 Hepatic Gene Transfer for Treatment of Hemophilias A & B KAY, MARK STANFORD UNIVERSITY CA $553,368
Gene Therapy 2017 NHLBI 5R01HL130040-02 In Vivo Hematopoietic Stem Cell Gene Therapy of Beta-Thalassemia LIEBER, ANDRE UNIVERSITY OF WASHINGTON WA $386,250
Gene Therapy 2017 OD 5R24OD022005-02 A Comprehensive Human cDNA Library For Functional Gene Replacement in Drosophila BELLEN, HUGO BAYLOR COLLEGE OF MEDICINE TX $668,865
Gene Therapy 2017 NIAID 5R01AI118500-03 Engineering T-cells with optimized anti-HIV chimeric antigen receptors and CCR5 disruption as a strategy to target HIV-infected cells WAGNER, THOR SEATTLE CHILDREN'S HOSPITAL WA $488,955
Gene Therapy 2017 NIGMS 1R35GM122564-01 Adeno-Associated Virus Gene Therapy Vectors: Molecular Interactions on Cell Entry CHAPMAN, MICHAEL OREGON HEALTH & SCIENCE UNIVERSITY OR $713,417
123


  • Download Readers:
  • Download Adobe PDF Reader
  • Download Microsoft PowerPoint Viewer
  • Download Microsoft Word Viewer
  • Download Microsoft Excel Viewer