Skip Navigation
 

Funding


RCDC

Project Listing by Category


Back to Estimates of Funding for Various Research, Condition, and Disease Categories (RCDC) Click the column headings to sort project listings.
  Help
CategoryFYFunding ICProject NumberSub Project #Project TitlePI NameOrg NameState / CountryAmount
Mucopolysaccharidoses (MPS) 2016 NICHD 4P01HD032652-18 5389 In Vivo Lentiviral Gene Therapy for Hurler Syndrome WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $240,173
Mucopolysaccharidoses (MPS) 2016 NICHD 4P01HD032652-18 5390 AAV Mediated Gene Therapy to the CNS for MPS I WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $250,166
Mucopolysaccharidoses (MPS) 2016 NICHD 4P01HD032652-18 5391 SB Transposons for Gene Therapy WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $278,730
Mucopolysaccharidoses (MPS) 2016 NICHD 4P01HD032652-18 5392 Administration WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $113,196
Mucopolysaccharidoses (MPS) 2016 NICHD 4P01HD032652-18 5393 Neuro-Histology & Behavior WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $183,539
Mucopolysaccharidoses (MPS) 2016 NICHD 4P01HD032652-18 5395 Research Animal Care and Medicine WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $132,868
Mucopolysaccharidoses (MPS) 2016 NINDS 5R01NS088766-02 Phenotypic effects of brain-directed enzyme therapy for Sanfilippo B syndrome DICKSON, PATRICIA LA BIOMED RES INST/ HARBOR UCLA MED CTR CA $310,283
Mucopolysaccharidoses (MPS) 2016 NINDS 5F31NS087747-02 Antisense-oligonucleotide-directed inhibition of nonsense-mediated mRNA decay NOMAKUCHI, TOMOKI COLD SPRING HARBOR LABORATORY NY $27,576
Mucopolysaccharidoses (MPS) 2016 NIAMS 5R03AR065142-03 Mechanisms of Vertebral Bone Disease in Mucopolysaccharidosis VII SMITH, LACHLAN UNIVERSITY OF PENNSYLVANIA PA $80,000
Mucopolysaccharidoses (MPS) 2016 NINDS 5R44NS088868-03 Sulfamidase Brain Drug Delivery in Sanfilippo Syndrome BOADO, RUBEN ARMAGEN TECHNOLOGIES, INC. CA $612,428
Mucopolysaccharidoses (MPS) 2016 NIDDK 5R01DK054481-20 Gene Therapy for Mucopolysaccharidosis CASAL, MARGRET UNIVERSITY OF PENNSYLVANIA PA $537,061
Mucopolysaccharidoses (MPS) 2016 NINDS 1R41NS092221-01A1 Engineering stem cells to make mucopolysaccharidosis IIIB EKINS, SEAN PHOENIX NEST, INC. NY $224,469
Mucopolysaccharidoses (MPS) 2016 NICHD 1R43HD087099-01 Enzyme Replacement Therapeutics for Rare Childhood Genetic Diseases: An ERT Delivery System that Mitigates Immune-sensitization RADIN, DAVID BIOSTRATEGIES, LC AR $225,000
Mucopolysaccharidoses (MPS) 2016 NINDS 4R01NS085381-04 Neuroimaging and Neuropathology of Mucopolysaccharidosis I DICKSON, PATRICIA LA BIOMED RES INST/ HARBOR UCLA MED CTR CA $304,460
Mucopolysaccharidoses (MPS) 2016 NINDS 1R21NS096044-01 Modified neural stem cells for glycosylation-independent treatment of MPS IIIB IACOVINO, MICHELINA LA BIOMED RES INST/ HARBOR UCLA MED CTR CA $260,587
Mucopolysaccharidoses (MPS) 2016 NINDS 1R01NS092671-01A1 Upregulation of Iduronidase Enzyme in MPSI Disease BROTHERS, SHAUN UNIVERSITY OF MIAMI SCHOOL OF MEDICINE FL $335,781
Mucopolysaccharidoses (MPS) 2016 NINDS 5R44NS083230-03 Enzyme replacement therapy for Sanfilippo A lysosomal rare disease RADIN, DAVID BIOSTRATEGIES, LC AR $659,425
Mucopolysaccharidoses (MPS) 2016 NIDDK 5R01DK067859-16 Multiplex Analysis of Inborn Errors of Metabolism GELB, MICHAEL UNIVERSITY OF WASHINGTON WA $597,597
Mucopolysaccharidoses (MPS) 2016 NINDS 2R42NS089061-02 Development and validation of therapy for mucopolysaccharidosis III EKINS, SEAN PHOENIX NEST, INC. NY $717,207
Mucopolysaccharidoses (MPS) 2016 NCATS 5U54NS065768-08 5620 Longitudinal Studies of Brain Structure and Function in MPS Disorders WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $45,099
Mucopolysaccharidoses (MPS) 2016 NIDDK 5U54NS065768-08 5620 Longitudinal Studies of Brain Structure and Function in MPS Disorders WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $71,411
Mucopolysaccharidoses (MPS) 2016 NINDS 5U54NS065768-08 5620 Longitudinal Studies of Brain Structure and Function in MPS Disorders WHITLEY, CHESTER UNIVERSITY OF MINNESOTA MN $51,450
Mucopolysaccharidoses (MPS) 2016 NCATS 5U54NS065768-08 5622 Longitudinal Study of Bone and Endocrine Disease in Children with MPS I, II, and VI: A Multi-Center Study of the Lysosomal Disease Network POLGREEN, LYNDA UNIVERSITY OF MINNESOTA MN $25,780
Mucopolysaccharidoses (MPS) 2016 NIDDK 5U54NS065768-08 5622 Longitudinal Study of Bone and Endocrine Disease in Children with MPS I, II, and VI: A Multi-Center Study of the Lysosomal Disease Network POLGREEN, LYNDA UNIVERSITY OF MINNESOTA MN $40,820
Mucopolysaccharidoses (MPS) 2016 NINDS 5U54NS065768-08 5622 Longitudinal Study of Bone and Endocrine Disease in Children with MPS I, II, and VI: A Multi-Center Study of the Lysosomal Disease Network POLGREEN, LYNDA UNIVERSITY OF MINNESOTA MN $29,410
Mucopolysaccharidoses (MPS) 2016 NCATS 5U54NS065768-08 5624 An Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I CHEN, AGNES UNIVERSITY OF MINNESOTA MN $12,080
Mucopolysaccharidoses (MPS) 2016 NIDDK 5U54NS065768-08 5624 An Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I CHEN, AGNES UNIVERSITY OF MINNESOTA MN $19,128
Mucopolysaccharidoses (MPS) 2016 NINDS 5U54NS065768-08 5624 An Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I CHEN, AGNES UNIVERSITY OF MINNESOTA MN $13,781
Mucopolysaccharidoses (MPS) 2016 NCATS 5U54NS065768-08 5630 Natural History Study for MPS IMC and MPS MID LEVY, PAUL UNIVERSITY OF MINNESOTA MN $2,045
Mucopolysaccharidoses (MPS) 2016 NIDDK 5U54NS065768-08 5630 Natural History Study for MPS IMC and MPS MID LEVY, PAUL UNIVERSITY OF MINNESOTA MN $3,238
Mucopolysaccharidoses (MPS) 2016 NINDS 5U54NS065768-08 5630 Natural History Study for MPS IMC and MPS MID LEVY, PAUL UNIVERSITY OF MINNESOTA MN $2,333
Mucopolysaccharidoses (MPS) 2016 NICHD 5F30HD081853-02 Novel Dried Blood Spot Mass Spectrometry Functional Assays for Lysosomal Acid Lipase and N-acetylgalactosamine-sulfate Sulfatases for Use in Newborn Screening MASI, SOPHIA UNIVERSITY OF WASHINGTON WA $48,576
Mucopolysaccharidoses (MPS) 2016 NICHD 1ZIAHD008927-05 Choroid plexus-mediated gene therapy for lysosomal storage disorders KALER, STEPHEN NIH $252,086


  • Download Readers:
  • Download Adobe PDF Reader
  • Download Microsoft PowerPoint Viewer
  • Download Microsoft Word Viewer
  • Download Microsoft Excel Viewer